Results 201 to 210 of about 200,281 (336)

Amyloidosis: Changing Approaches and Outcomes

, 2012
Lawrence Rice, Kelty R. Baker
openalex   +2 more sources

Spontaneous bilateral kidney rupture during autologous stem cell transplantation in a patient affected by amyloidosis [PDF]

, 2010
Michele Ferrannini, Gisella Vischini, G De Angelis, Konstantinos Giannakakis, William Arcese   +4 more
openalex   +1 more source

A new staging system for cardiac transthyretin amyloidosis

European Heart Journal, 2018
J. Gillmore, T. Damy, M. Fontana, M. Hutchinson, H. Lachmann, A. Martinez-Naharro, C. Quarta, T. Rezk, C. Whelan, E. Gonzalez-Lopez, T. Lane, J. Gilbertson, D. Rowczenio, A. Petrie, P. Hawkins   +14 more
semanticscholar   +1 more source

State‐of‐the‐Art on Model‐Informed Drug Development Approaches for Pediatric Rare Diseases

CPT: Pharmacometrics &Systems Pharmacology, EarlyView.
ABSTRACT Pediatric rare diseases present unique challenges for drug development due to small patient populations, ethical constraints on clinical trial design, and limited prospectively defined natural history data. Model‐Informed Drug Development (MIDD) has emerged as a powerful paradigm to address these challenges by leveraging quantitative methods ...
Rajesh Krishna, Amitava Mitra, Matthew L. Zierhut, Lilly East, Chandra Durairaj   +4 more
wiley   +1 more source

Localized cutaneous nodular amyloidosis from insulin injections in a 40-year-old woman. [PDF]

CMAJ
Zhuang M, Vaziri M, Sandhu N.
europepmc   +1 more source

Nanoscale Analysis beyond Imaging by Atomic Force Microscopy: Molecular Perspectives on Oncology and Neurodegeneration

Small Science, EarlyView.
Cancer and neurodegeneration share interconnected nanosized molecular pathways. Novel nanobiomedicine approaches promise targeted biomarkers and therapies. Atomic force microscopy (AFM) is invaluable to characterize nanosized biomolecular processes beyond imaging.
Carlos Marcuello, KeeSiang Lim, Giacomo Nisini, Vadim S. Pokrovsky, João Conde, Francesco Simone Ruggeri   +5 more
wiley   +1 more source

Intracellular amyloidosis in peripheral nerve and skeletal muscle. [PDF]

J Neuropathol Exp Neurol
Grafham GK, Mak G, Grant S, Murphy A, Baker SK, Tarnopolsky M, Lu JQ.   +6 more
europepmc   +1 more source

Lipid Nanoparticles for Delivery of CRISPR Gene Editing Components

Small Methods, EarlyView.
The review presents a comprehensive overview of each component of lipid nanoparticles（LNPs）and their effects on editing efficiency. It specifically highlights strategies for achieving non‐liver delivery, aiming for broader applications in gene editing. Furthermore, this review summarizes the applications of LNPs in gene editing and offers insights for ...
Fan Wu, Nei Li, Yudian Xiao, Rohan Palanki, Hannah Yamagata, Michael J. Mitchell, Xuexiang Han   +6 more
wiley   +1 more source

The Healthcare Amyloidosis European Registry (HEAR): design of a national registry with a European extension strategy, and foundation of the F-CRIN GRACE network. [PDF]

Orphanet J Rare Dis
Réant P, Kharoubi M, Donal E, Bauer F, Bézard M, Bisson A, Bodez D, Bouchot O, Cariou E, Charron P, Costa J, Courand PY, Dagrenat C, Delelis F, Duval AJ, Eicher JC, Fraix A, Gellen B, Gueffet JP, Guijarro D, Habib G, Hagège A, Huttin O, Jaccard A, Jeanneteau J, Legallois D, Logeart D, Legrand L, Inamo J, Marguerit L, Mirailles R, Pezel T, Piriou N, Roubille F, Mouhat B, Trésorier R, Von Hunolstein JJ, Taieb C, Salvat M, Zaroui A, Lairez O, Damy T.   +41 more
europepmc   +1 more source

Multifocal pulmonary amyloidosis mimicking metastases

Badriya Al Suqri
openalex   +1 more source