Self‐Reported Health‐Related Quality of Life (HRQoL) in Adults With Urea Cycle Disorders
ABSTRACT Multiple studies have assessed Health‐Related Quality of Life (HRQoL) in children with urea cycle disorders (UCDs); investigations in adults with the same disorders are rarer. Understanding the variables that modify self‐reported HRQoL has become increasingly important as novel treatments are developed, with clinically meaningful endpoints ...
Curtis R. Coughlin II +25 more
wiley +1 more source
Successful Reswitching of Thrombopoietin Receptor Agonists: Two Cases of Immune Thrombocytopenia and Severe Aplastic Anemia. [PDF]
Itoh K +7 more
europepmc +1 more source
Real‐World Effectiveness and Safety of Pegzilarginase Treatment in Arginase 1 Deficiency
ABSTRACT Pegzilarginase is the first disease‐modifying drug for arginase 1 deficiency. In clinical trials, pegzilarginase effectively normalised plasma arginine (pArg), which was associated with clinically relevant improvements in neuromotor outcomes. We report from a French early access scheme the first report on experience from pegzilarginase therapy
Anaïs Brassier +10 more
wiley +1 more source
From Plastic Waste to Pharmaceutical Precursors: PET Upcycling Through Ruthenium Catalyzed Semi-Hydrogenation. [PDF]
Kulyabin PS +12 more
europepmc +1 more source
Quantification of natural attenuation using analytical-chemical tools [PDF]
Reitzel, Lotte
core
ABSTRACT The hydrophilic–lipophilic difference (HLD) for ionic surfactant microemulsions (μEs) can be interpreted as the curvature normalized by the tail length parameter (L), if it is corrected by a factor “bi”, bi·HLD = HLDcurv = HLDbi = bi·ln(S) – kbi·EACN + Ccbi, with bi and kbi representing the curvature sensitivity to changes in salinity (S, g ...
Edgar Acosta +2 more
wiley +1 more source
Successful Treatment of Primary Poor Graft Function After Haploidentical Hematopoietic Stem Cell Transplantation With Low-Dose Decitabine Followed by Donor Lymphocyte Infusion and Eltrombopag. [PDF]
Yuan J +8 more
europepmc +1 more source
This review examines how hybrid modification strategies enhance the structural design and environmental performance of metal–organic frameworks (MOFs). It outlines key synthesis routes, functionalization approaches, and integration with complementary materials, highlighting advances in pollutant removal, sensing, and sustainable remediation.
Samar H. Elagamy +3 more
wiley +1 more source
Intramolecular asymmetric propargylation of esters and imides: C-H functionalisation enables stereocontrolled access to UCS1025A. [PDF]
Corcoran JC +4 more
europepmc +1 more source
Dental composites: a comprehensive review on formulation, properties and recent developments
Dental composites are essential in modern restorative dentistry; this review covers their development, composition, key properties and recent advances, highlighting new technologies for optimizing materials and improving clinical outcomes. Abstract Dental composites have evolved considerably since their introduction, becoming the cornerstone of modern ...
Rayenne Latoui +2 more
wiley +1 more source

