Results 191 to 200 of about 800,688 (313)

Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito, Kamal Benguerba, Ken Tsuchida, Kazushige Yazawa, Isao Tsumiyama, Hiromitsu Kayama, Sandra P. Reyna, Farid Khan, Richard S. Finkel   +8 more
wiley   +1 more source

Best practices framework for using 16S rRNA gene sequencing in poultry microbiota research. [PDF]

Poult Sci
Lyte JM, Seyoum MM, Ayala D, Kers JG, Caputi V, Johnson T, Zhang L, Rehberger J, Zhang G, Dridi S, Hale B, De Oliveira JE, Grum D, Smith AH, Robinson K, Kogut M, Olson EG, Ricke SC, Ballou A, Potter B, Proszkowiec-Weglarz M.   +20 more
europepmc   +1 more source

A Two‐Stage Questionnaire and Actigraphy Screening for iRBD in a Multicenter Retrospective Cohort

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Isolated rapid‐eye‐movement sleep behavior disorder is a prodromal marker of synucleinopathies. However, most cases remain undiagnosed due to the insufficient predictive value of questionnaires and limited access to confirmatory video‐polysomnography. We assessed a two‐stage screening strategy combining a brief questionnaire on rapid‐
Caleb A. Massimi, Giorgio Ricciardiello Mejia, Andre Metzger, Kang Hyun Ryu, Salonee Marwaha, Eva Grzegorczyk, Li Zhou, Eliana Jacobs, Boris Gilyadov, Claudia Kunney, Liqhwa Ncube, Ankit Parekh, Emmanuel Mignot, Fanny M. Elahi, Joseph Winer, Kathleen Poston, Andreas Brink‐Kjaer, Emmanuel H. During   +17 more
wiley   +1 more source

BEST PRACTICES

Espacio, Tiempo y Forma. Serie VII, Historia del Arte, 2016
Revista ETF VII Revista ETF VII
doaj   +1 more source

Best Practices and Considerations for Applying Multiple Linear Regression in Organic Chemistry Research. [PDF]

J Org Chem
LeSueur A, Bianchi P, Gallarati S, Lefave SJ, Sigman MS.   +4 more
europepmc   +1 more source

Neurochemical Endpoints to Inform Early‐Stage Trials of Spinocerebellar Ataxia 2 and 3 in a Multisite Setting

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Neurochemical levels measured by brain MR spectroscopy (MRS) have been proposed as endpoints for clinical trials in early‐stage spinocerebellar ataxia (SCA) trials. We tested their trial‐readiness by quantifying neurochemicals in three affected brain regions in early‐stage cohorts of SCA2 and SCA3, examining their reproducibility in ...
James M. Joers, Yaqiao Wei, Dinesh K. Deelchand, Adam Berrington, Young Woo Park, Guita Banan, Michal Povazan, Jens T. Rosenberg, André J. W. van der Kouwe, Tetsuo Ashizawa, Khalaf O. Bushara, Chiadi U. Onyike, Sub H. Subramony, Jeremy D. Schmahmann, Brian J. Soher, Peter B. Barker, Thomas H. Mareci, Eva‐Maria Ratai, Lynn E. Eberly, Gülin Öz   +19 more
wiley   +1 more source

Development of Clinical Practice Guidelines and Primary Care Referral Pathways for the Management of Otorhinolaryngological Conditions in Pakistan

International Archives of Otorhinolaryngology
Alina Pervez, Russell Seth Martins, Huzaifa Moiz, Abbas Raza Syed, Muneeb Khan, Nashia Ali Rizvi, Mohsin Ali Mustafa, Muhammad Taha Nasim, Alina Abdul Rehman, Shayan Khalid, Saif Ur Rehman, Sarah Nadeem, Adil H. Haider, Shabbir Akhtar   +13 more
doaj   +1 more source

Refining Nail Surgery: Clinical Pearls and Best Practices. [PDF]

Ann Dermatol
Jung JW, Oh J, Oh BH.
europepmc   +1 more source

Cognitive and Neuroimaging Divergence Between Juvenile and Adult FUS Amyotrophic Lateral Sclerosis

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Amyotrophic lateral sclerosis (ALS) is a neurodegenerative disorder characterized by progressive motor neuron degeneration. Fused in sarcoma (FUS)‐associated juvenile ALS (jALS) represents a distinct and aggressive subgroup with rapid deterioration and poor prognosis.
Alexandra V. Jürs, Marcel Naumann, Annaliis Lehto, Hanna Schön, Jens Kurth, Johannes Prudlo, Andreas Hermann, Elisabeth Kasper   +7 more
wiley   +1 more source

Best practices for moving from correlation to causation in ecological research. [PDF]

Nat Commun
Correia HE, Dee LE, Byrnes JEK, Fieberg JR, Fortin MJ, Glymour C, Runge J, Shipley B, Shpitser I, Siegel KJ, Sugihara G, von Holle B, Ferraro PJ.   +12 more
europepmc   +1 more source