Results 141 to 150 of about 21,255 (259)
Introduction In recent years, the treatment of spinal muscular atrophy (SMA), a rare disease, has significantly progressed, improving patients' survival and overall quality of life. However, current SMA treatments are expensive, and some (nusinersen) are very inconvenient for patients.
Andrej Belančić +4 more
wiley +1 more source
Environmental impacts from European food consumption can be reduced with carbon pricing or a value-added tax reform. [PDF]
Plinke C, Sureth M, Kalkuhl M.
europepmc +1 more source
Financial Feasibility of BPaL(M) Under Pretomanid Price Scenarios - China, 2023-2024. [PDF]
Ren J +10 more
europepmc +1 more source
Regulators use expedited approval pathways to speed market approval and patient access to promising new drugs. However, there is uncertainty about whether these pathways are successful in approving drugs with significant therapeutic advantages. This systematic review aims to examine the safety, effectiveness and cost‐effectiveness of drugs approved via
Ashleigh Hooimeyer +4 more
wiley +1 more source
Land Finance and fiscal rules: An estimated DSGE model for Hong Kong. [PDF]
Zhang W, Liu Z.
europepmc +1 more source
Precision medicine in paediatrics: Progress and priorities
Precision medicine is revolutionizing personalized healthcare, advancing both diagnostics and therapeutics at an unprecedented pace. Reviewing the paediatric applications of pharmacometrics, pharmacogenomics and advanced therapy medicinal products highlights not only the relevance of these exciting innovations to frontline care but also the significant
Nicola Husain +3 more
wiley +1 more source
Accuracy of Budget Impact Projections in Bulgarian Health Technology Assessment: A Five-Year Validation Study (2020-2025). [PDF]
Kostadinov K +5 more
europepmc +1 more source
Aims GLP‐1 medicines provide substantial cardio‐renal benefits for type 2 diabetes (T2D) and are increasingly used for weight loss. Most high‐income countries subsidize access for T2D with restrictions; use outside of these restrictions occurs through private prescriptions. Despite strong consumer demand, the extent of private access to GLP‐1 medicines
Michael O. Falster +10 more
wiley +1 more source
Physician agency in China: evidence from physicians' responses to financial pressure during the COVID-19 pandemic. [PDF]
Zhang Q.
europepmc +1 more source
THEORIZATION OF THE BUDGETING FOR MILITARY EXPENDITURES
openaire +2 more sources

