Results 231 to 240 of about 902,578 (275)

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24‐Month Follow‐Up From the Italian Registry

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane, Giorgia Coratti, Chiara Cutrì, Antonio Varone, Riccardo Masson, Adele D'Amico, Valeria Sansone, Sonia Messina, Federica Ricci, Chiara Ticci, Claudio Bruno, Caterina Agosto, Francesca Benedetti, Antonella Pini, Sabrina Siliquini, Massimiliano Filosto, Alberto Zambon, Ilaria Bitetti, Maria Rosaria Manna, Claudia Dosi, Riccardo Zanin, Stefano Parravicini, Roberto De Sanctis, Giulia Stanca, Michela Catteruccia, Michele Tosi, Irene Mizzoni, Emilio Albamonte, Valentina Franchino, Maria Sframeli, Ilaria Cavallina, Elena Procopio, Michele Sacchini, Simone Morando, Noemi Brolatti, Federica Trucco, Gaia Scarpini, Elena Briganti, Beatrice Berti, Concetta Palermo, Daniela Leone, Stefano C. Previtali, Eugenio Mercuri, the ITASMAC working group   +43 more
wiley   +1 more source

100 m climate and heat stress data up to 2100 for 142 cities around the globe. [PDF]

Data Brief
Souverijns N, Lauwaet D, Lejeune Q, Kropf CM, Yeung KL, Nath S, Schleussner CF.   +6 more
europepmc   +1 more source

Digital Inventory of Swiss Construction Systems. [PDF]

Sci Data
Arceo A, Bastien-Masse M, Lambec B, Fivet C.   +3 more
europepmc   +1 more source

Policymaker-led scenarios and public dialogue facilitate energy demand analysis for net-zero futures. [PDF]

Nat Energy
Sharmina M, Broad O, Barrett J, Brand C, Garvey A, Kennard H, Norman J, Price J, Pye S, Snape J, White E.   +10 more
europepmc   +1 more source

Data-Driven Operational Bounds of Transmembrane Pressure for Modelling and Digital Twin Development in Haemodialysis and Haemodiafiltration. [PDF]

Bioengineering (Basel)
Dinu A, Frunzete M, Mihailovschi D.
europepmc   +1 more source

COLLECTiEF dataset: A high-resolution indoor environmental dataset from European buildings across diverse climates supporting thermal, air-quality, and visual-comfort assessments. [PDF]

Data Brief
Campodonico-Avendano IA, Erba S, Papadopoulos P, Carlucci S, Luparelli A, Ingrosso A, Tresoldi G, Shahid MS, Wurtz F, Delinchant B, Leinan PM, Cera S, Riederer P, Solli R, Moazami A, Aghaei M.   +15 more
europepmc   +1 more source

Research on Radio Altimetry in Urban Environments Based on Electromagnetic Simulation Echo Modeling Technology. [PDF]

Sensors (Basel)
Xiong J, Xie X, Guan X, Xu Y, Li C.
europepmc   +1 more source