ADAPT NXT: Fixed Cycles or Every‐Other‐Week IV Efgartigimod in Generalized Myasthenia Gravis
ABSTRACT Objective This phase 3b, open‐label, randomized ADAPT NXT study investigated the efficacy, safety, and tolerability of efgartigimod administered in either a fixed cycles dosing regimen (3 cycles of 4 once‐weekly infusions, with 4 weeks between cycles) or a cycle followed by every‐other‐week (Q2W) dosing.
Ali A. Habib+16 more
wiley +1 more source
Empirical likelihood confidence interval for sensitivity to the early disease stage. [PDF]
Rahman H+2 more
europepmc +1 more source
Confidence intervals and standard errors for ratios of normal variables [PDF]
William P. Dunlap, N. Clayton Silver
openalex +1 more source
Myostatin Levels in SMA Following Disease‐Modifying Treatments: A Multi‐Center Study
ABSTRACT Objective This study investigated myostatin levels in SMA patients receiving disease‐modifying therapies (DMTs) to understand their relationship with treatment duration and functional status. Methods Our study includes both cross‐sectional and longitudinal analyses of myostatin levels in treated SMA patients.
Fiorella Piemonte+23 more
wiley +1 more source
Calculating and Comparing the Annualized Relapse Rate and Estimating the Confidence Interval in Relapsing Neurological Diseases. [PDF]
Akaishi T, Ishii T, Aoki M, Nakashima I.
europepmc +1 more source
Confidence intervals with fixed proportional accuracy [PDF]
Michael Woodroofe
openalex +1 more source
ABSTRACT Objective People with HIV (PWH) on antiretroviral therapy (ART) still experience neurocognitive dysfunction and accelerated brain volume loss. To assess whether the serotonergic and dopaminergic systems are affected, we used [11C]DASB positron emission tomography (PET) to assess presynaptic serotonergic function and [18F]FDOPA PET to measure ...
Chuen‐Yen Lau+12 more
wiley +1 more source
The Use of Sample Quasi-Ranges in Setting Confidence Intervals for the Population Standard Deviation
F. C. Leone, Y. H. Rutenberg, C. W. Topp
openalex +2 more sources
Military Service Roles and ALS Among Veterans: A Matched Case–Control Study
ABSTRACT While military service is an established risk factor for amyotrophic lateral sclerosis (ALS), it remains unclear whether this association is linked to combat. We conducted a matched case–control study comparing 191 ALS patients who were veterans of the Israeli Defense Forces (IDF) with known military service type and 1910 matched controls. The
Asaf Honig+4 more
wiley +1 more source
A Monte Carlo Study of Confidence Interval Methods for Generalizability Coefficient. [PDF]
Jiang Z+5 more
europepmc +1 more source