Results 281 to 290 of about 110,072 (307)

DMD

Neurology Today, 2001
openaire   +1 more source

DMD

Neurology Today, 2004
openaire   +1 more source

Sarepta’s DMD gene therapy falls flat

Nature Reviews Drug Discovery, 2021
exaly  

DMD CLINICAL

Neuromuscular Disorders, 2019
M. Mah, M. Slawinski, L. Cripe, E. Camino, S. Al-Zaidy, S. Hassan, J. Jackson, L. Lowes, M. Iammarino, N. Miller, L. Alfano, K. Lehman, J. Mendell, K. Hor   +13 more
openaire   +1 more source

Therapeutic approaches for Duchenne muscular dystrophy

Nature Reviews Drug Discovery, 2023
Thomas C Roberts, Kay E Davies
exaly  

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Lancet, The, 2017
Craig M Mcdonald, Craig Campbell, Richard S Finkel   +2 more
exaly  

DMD

2008
openaire   +1 more source

Complete cloning of the duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals

Cell, 1987
Eric P Hoffman, Anthony P Monaco
exaly  

The SINE Compound KPT-350 Blocks Dystrophic Pathologies in DMD Zebrafish and Mice

Molecular Therapy, 2020
Andrea L Reid, Louis M Kunkel, Sergio Armando Villalta   +2 more
exaly  

The TREAT-NMD DMD Global Database: Analysis of More than 7,000 Duchenne Muscular Dystrophy Mutations

Human Mutation, 2015
David Salgado, MARIA EUGENIA FONCUBERTA, Kyriaki Kekou   +2 more
exaly