Results 141 to 150 of about 30,575 (221)

Early Cardiac Manifestations as the Initial Presentation of Duchenne Muscular Dystrophy in Infancy. [PDF]

Cureus
Shatarat F, Alkasasbeh J, Shatarat R, Tarawneh S.   +3 more
europepmc   +1 more source

YAP Acts as a Negative Regulator of Mini Utrophin-Based Gene Therapy for Duchenne Muscular Dystrophy in Mdx Mice. [PDF]

Int J Mol Sci
Li Z, Song Y.
europepmc   +1 more source

Systematic Literature Reviews of Health-State Utility Values, Costs, and Healthcare Resource Use in Duchenne Muscular Dystrophy. [PDF]

J Health Econ Outcomes Res
Yip CY, Kemadjou EN, Stewart D, Shapiro H, Macmillan T.   +4 more
europepmc   +1 more source

Exosome-Mediated Benefits of Cell Therapy in Mouse and Human Models of Duchenne Muscular Dystrophy. [PDF]

Stem Cell Reports
Aminzadeh MA, Rogers RG, Fournier M, Tobin RE, Guan X, Childers MK, Andres AM, Taylor DJ, Ibrahim A, Ding X, Torrente A, Goldhaber JM, Lewis M, Gottlieb RA, Victor RA, Marbán E.   +15 more
europepmc   +1 more source

Management of Duchenne Muscular Dystrophy in Clinical Practice: A Survey-Based Study in Spain. [PDF]

Neurol Ther
Ortez C, Branas-Pampillón M, Fernandez JA, Guillen E, Terrancle Á, Maurino J, Montolio M, Camacho A.   +7 more
europepmc   +1 more source

Successful In Vitro Modification of the <i>Dmd</i> Gene Using Prime Editing. [PDF]

Cells
Siddika A, Husseiny FE, Rousseau J, Tremblay JP.   +3 more
europepmc   +1 more source

Duchenne Muscular Dystrophy: Contemporary Therapeutic Options and Real-World Challenges in Treatment Selection. [PDF]

Muscles
Pesco MT, Öztürk GZ, Bhadola SC, Chrzanowski SM, Gushchina LV, D'Ambrosio ES.   +5 more
europepmc   +1 more source

Vamorolone for Duchenne Muscular Dystrophy: A Cross-Trial Efficacy Comparison With Classic Corticosteroids From the FOR-DMD Trial. [PDF]

Neurology
Clemens PR, Berglund A, Schiava M, James MK, McDermott MP, Bushby K, Lampa E, Rochford ETJ, Ward LM, Griggs RC, Hoffman EP, Guglieri M.   +11 more
europepmc   +1 more source

An Assessment of Paediatricians' Knowledge and Perspectives of Duchenne Muscular Dystrophy in Oman. [PDF]

Sultan Qaboos Univ Med J
Al Jabri Z, Alsawaie M, Saki Malehi A, Al Futaisi A, Al-Amrani F.   +4 more
europepmc   +1 more source

Physical Activity and Quality of Life Among Caregivers of Children with Duchenne Muscular Dystrophy. [PDF]

Healthcare (Basel)
Yiğit S, Akgün İ, Coşkun K, Çınar MA, Usgu S, Perk P.   +5 more
europepmc   +1 more source