Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy. [PDF]
Lochmüller H +14 more
europepmc +1 more source
Assessing the Relationship of Quality of Life With Functional Status in a Large Cohort of Adult Patients With Neuromuscular Disorders. [PDF]
Wong KSW +18 more
europepmc +1 more source
Management of adrenal insufficiency risk after long-term systemic glucocorticoid therapy in Duchenne muscular dystrophy: Clinical practice recommendations [PDF]
Bowden, Sasigarn A +3 more
core +1 more source
Burden of Duchenne muscular dystrophy in Australia: a scoping review. [PDF]
Lee E, Choi S, Kim H.
europepmc +1 more source
Caregiver burden in Duchenne muscular dystrophy in Europe, Japan, and the United States - a real-world study. [PDF]
Strober J +11 more
europepmc +1 more source
Rethinking Corticosteroid Therapy in Pediatric Neurology. [PDF]
Lin WS.
europepmc +1 more source
Acute Gastric Dilatation in a 16-Year-Old Patient With Duchenne Muscular Dystrophy: A Case Report and an Updated Literature Review. [PDF]
Novoa Garnica C +4 more
europepmc +1 more source

