Results 251 to 257 of about 71,442 (257)

Therapeutic approaches for Duchenne muscular dystrophy

Nature reviews. Drug discovery, 2023
T. Roberts, Matthew J. A. Wood, Kay E. Davies   +2 more
semanticscholar   +1 more source

Dystrophin: The protein product of the duchenne muscular dystrophy locus

Cell, 1987
Eric P. Hoffman, Robert H. Brown, Louis M. Kunkel   +2 more
semanticscholar   +1 more source

Emerging therapies for Duchenne muscular dystrophy

Lancet Neurology, 2022
Theodora Markati, M. Oskoui, M. Farrar, T. Duong, N. Goemans, L. Servais   +5 more
semanticscholar   +1 more source

Therapeutic developments for Duchenne muscular dystrophy

Nature Reviews Neurology, 2019
I. Verhaart, A. Aartsma-Rus
semanticscholar   +1 more source

Complete cloning of the duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals

Cell, 1987
M. Koenig, E. P. Hoffman, C. Bertelson, A. Monaco, C. Feener, L. Kunkel   +5 more
semanticscholar   +1 more source

Adenine base editing in mouse embryos and an adult mouse model of Duchenne muscular dystrophy

Nature Biotechnology, 2018
Seuk-Min Ryu, T. Koo, Kyoungmi Kim, Kayeong Lim, Gayoung Baek, Sang-Tae Kim, H. Kim, Daesik Kim, Hyunji Lee, Eugene Chung, Jin-Soo Kim   +10 more
semanticscholar   +1 more source

Detection of collagens by multispectral optoacoustic tomography as an imaging biomarker for Duchenne muscular dystrophy

Nature Medicine, 2019
Adrian P. Regensburger, L. Fonteyne, J. Jüngert, A. Wagner, Teresa Gerhalter, A. Nagel, R. Heiss, F. Flenkenthaler, M. Qurashi, M. Neurath, N. Klymiuk, E. Kemter, T. Fröhlich, M. Uder, J. Woelfle, W. Rascher, R. Trollmann, E. Wolf, M. Waldner, F. Knieling   +19 more
semanticscholar   +1 more source