Results 191 to 200 of about 27,913 (221)

Pharmacotherapy of Duchenne Muscular Dystrophy

2019
Drug development and pharmacotherapy of rare pediatric diseases have significantly expanded over the last decade, in part due to incentives and financial support provided by governments, regulators, and nonprofit foundations. Duchenne muscular dystrophy (DMD) is among the most common rare pediatric disorders, and clinical trials of therapeutic ...
openaire   +2 more sources

Comparative proteomic analyses of Duchenne muscular dystrophy and Becker muscular dystrophy muscles: changes contributing to preserve muscle function in Becker muscular dystrophy patients

Journal of Cachexia, Sarcopenia and Muscle, 2020
Daniele Capitanio, Cecilia Gelfi, Manuela Moriggi   +2 more
exaly  

Delayed Diagnosis in Duchenne Muscular Dystrophy: Data from the Muscular Dystrophy Surveillance, Tracking, and Research Network (MD STARnet)

Journal of Pediatrics, 2009
Paul Romitti, Timothy Miller, Katherine Mathews   +2 more
exaly  

Duchenne Muscular Dystrophy

Pediatrics In Review, 2006
openaire   +2 more sources

miRNAs as serum biomarkers for Duchenne muscular dystrophy

EMBO Molecular Medicine, 2011
Enrico Bertini, Irène Bozzoni, Ivano Legnini   +2 more
exaly  

Asynchronous remodeling is a driver of failed regeneration in Duchenne muscular dystrophy

Journal of Cell Biology, 2014
Eric Hoffman, Jianhua Xuan, Kanneboyina Nagaraju   +2 more
exaly  

Prevention of Pulmonary Morbidity for Patients With Duchenne Muscular Dystrophy

Chest, 1997
Yuka Ishikawa, John Bach, Heakyung Kim   +2 more
exaly  

Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary

American Journal of Respiratory and Critical Care Medicine, 2017
David Birnkrant, Hemant Sawnani, Erik Henricson   +2 more
exaly  

Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study

Lancet, The, 2018
Mathula Thangarajh, Monique Ryan, Eric Hoffman   +2 more
exaly  

Emerging drugs for Duchenne muscular dystrophy

Expert Opinion on Emerging Drugs, 2012
Louise R Rodino-Klapac
exaly