Results 281 to 290 of about 71,159 (294)

Genetic and pharmacologic inhibition of mitochondrial-dependent necrosis attenuates muscular dystrophy

Nature Medicine, 2008
Douglas P Millay, Christopher P Baines, Elisabeth R Barton   +2 more
exaly  

Spinal muscular atrophy — insights and challenges in the treatment era

Nature Reviews Neurology, 2020
Eugenio Mercuri, Maria Carmela Pera, Richard S Finkel   +2 more
exaly  

Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy

Nature Medicine, 2020
exaly  

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly  

Advances in therapy for spinal muscular atrophy: promises and challenges

Nature Reviews Neurology, 2018
Ewout J N Groen, Kevin Talbot, Thomas Gillingwater   +2 more
exaly  

Duchenne Muscular Dystrophy

2019
Charles V. Pollack, Richard M. Cantor, Victoria G. Riese   +2 more
openaire   +2 more sources

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

Lancet Neurology, The, 2010
David J Birnkrant, Laura E. Case, Paula R Clemens   +2 more
exaly  

Short Telomeres and Stem Cell Exhaustion Model Duchenne Muscular Dystrophy in mdx/mTR Mice

Cell, 2010
Alessandra Sacco, Foteini Mourkioti, Scott L Delp   +2 more
exaly  

Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management

Lancet Neurology, The, 2018
David J Birnkrant, Carla M Bann, Benjamin A Alman   +2 more
exaly  

A mutation-independent approach for muscular dystrophy via upregulation of a modifier gene

Nature, 2019
Dwi U Kemaladewi, Steven Erwood, Steven A Prescott   +2 more
exaly