Results 231 to 240 of about 48,181 (245)

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

Nature Medicine, 2003
Christopher J Mann, Susan Fletcher
exaly  

The lncRNA H19 alleviates muscular dystrophy by stabilizing dystrophin

Nature Cell Biology, 2020
Yaohua Zhang, Yajuan Li, Qingsong Hu
exaly  

Multiplex CRISPR/Cas9-based genome editing for correction of dystrophin mutations that cause Duchenne muscular dystrophy

Nature Communications, 2015
Pratiksha I Thakore, William H Majoros, Timothy E Reddy   +2 more
exaly  

Muscle-specific CRISPR/Cas9 dystrophin gene editing ameliorates pathophysiology in a mouse model for Duchenne muscular dystrophy

Nature Communications, 2017
Guy L Odom, Michael P Phelps, R David Hawkins   +2 more
exaly  

Dystrophin and mutations: one gene, several proteins, multiple phenotypes

Lancet Neurology, The, 2003
Silvia Torelli, Alessandra Ferlini
exaly  

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

Lancet Neurology, The, 2009
V Arechavala-Gomeza, Sebahattin Cirak, Linda J Popplewell   +2 more
exaly  

Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy

Science Translational Medicine, 2017
Leonela Amoasii, Chengzu Long, Hui Li
exaly  

Dystrophin expression in muscle stem cells regulates their polarity and asymmetric division

Nature Medicine, 2015
Nicolas A Dumont, Yu Xin Wang, Julia von Maltzahn   +2 more
exaly  

The Dystrophin Glycoprotein Complex

Circulation Research, 2004
Elizabeth M Mcnally
exaly  

SNF-6 is an acetylcholine transporter interacting with the dystrophin complex in Caenorhabditis elegans

Nature, 2004
Hongkyun Kim, Matthew J Rogers
exaly