Results 171 to 180 of about 149,854 (224)

Five‐Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: A Phase 1/2a Study

Muscle &Nerve, EarlyView.
ABSTRACT Aims We report 5‐year results from a phase 1/2a study of delandistrogene moxeparvovec, a recombinant adeno‐associated virus serotype rh74 vector‐based gene therapy for Duchenne muscular dystrophy (DMD), with post hoc analyses contextualizing functional outcomes. Methods Four ambulatory patients with DMD (≥ 4–< 8 years at enrollment) entered an
Jerry R. Mendell, Zarife Sahenk, Linda P. Lowes, Megan A. Iammarino, Lindsay N. Alfano, Craig M. McDonald, James E. Signorovitch, Jim Jin, Jing Li, Stefanie Mason, Louise R. Rodino‐Klapac   +10 more
wiley   +1 more source

Celebrating the 65th Anniversary of the Journal of Clinical Pharmacology. [PDF]

J Clin Pharmacol
van den Anker J.
europepmc   +1 more source

Reconsidering Volume‐Based Drug Procurement Policy: The Consequences of Manufacturers' Optimal Production Planning and Breach Strategies

Naval Research Logistics (NRL), EarlyView.
ABSTRACT This paper examines the impacts of Volume‐Based Procurement (VBP) policies on pharmaceutical supply chains, with a focus on the strategic behaviors of manufacturers. VBP aims to reduce costs and stabilize supplies by centralizing procurement through competition based on volumes and prices.
Nani Zhou, Tong Wang, Guohua Wan
wiley   +1 more source

Exploring staff and service user experiences of personality disorder services in open prisons: A qualitative study of Pathways Enhanced Resettlement Support. [PDF]

PLoS One
Mathlin G, Jones H, Lewis C, Cooper C, Freestone M.   +4 more
europepmc   +1 more source

On‐Time Meal Delivery Assisted by Drone Resupply

Naval Research Logistics (NRL), EarlyView.
ABSTRACT Ensuring timely delivery is crucial with the increasing competition in online meal delivery services. This requires the industry to adopt new technologies and the corresponding operational models, including the use of drones. Concerning the desired features of meal delivery, such as safety and reliability, we propose an operational model that ...
Wenqian Liu, Lindong Liu, Xiangtong Qi
wiley   +1 more source

Lectotypifications and taxonomic changes in the holoparasitic Orobanchaceae

Nordic Journal of Botany, EarlyView.
Based on further extensive studies of specimens in various herbaria, lectotypes are designated for many taxa of holoparasitic Orobanchaceae. In particular, 47 names in the genera Boschniakia (incl. Xylanche), Cistanche, Orobanche, Phelipanche and Phelypaea are lectotypified.
Holger Uhlich, Stefan Rätzel, Óscar Sánchez Pedraja, Renata Piwowarczyk, Valerio Lazzeri, Patrice Descombes   +5 more
wiley   +1 more source

Beneficiary feedback mechanisms: Exploring ways to systematically integrate community feedback in mass drug administration delivery for NTDs. [PDF]

PLoS Negl Trop Dis
Mathewson JD, Aardewijn C, de Vlas SJ, Matungwa DJ, Bakker MI.   +4 more
europepmc   +1 more source

An Unusual Patchy Alopecia in a 15th Century Altarpiece From Colmar, France

JEADV Clinical Practice, Volume 5, Issue 2, Page 690-691, June 2026.
Nicolas Kluger
wiley   +1 more source