Results 311 to 320 of about 460,260 (336)

ENZYME REPLACEMENT THERAPY

1979
Ernest Beutler, George L. Dale
openaire   +1 more source

Favourable effect of early versus late start of enzyme replacement therapy on plasma globotriaosylsphingosine levels in men with classical Fabry disease.

Molecular Genetics and Metabolism, 2017
M. Arends, F. Wijburg, C. Wanner, F. Vaz, A. V. van Kuilenburg, D. Hughes, M. Biegstraaten, A. Mehta, C. Hollak, M. Langeveld   +9 more
semanticscholar   +1 more source

Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry

American Journal of Medicine, 2002
Neal J Weinreb, Ari Zimran
exaly  

Enzyme Replacement Therapy: A Review and Its Role in Treating Lysosomal Storage Diseases.

Pediatric annals, 2018
Mindy H. Li
semanticscholar   +1 more source

Cardiovascular abnormalities in late-onset Pompe disease and response to enzyme replacement therapy

Genetics in Medicine, 2011
Priya Kishnani, Sara Pasquali, Jennifer Li   +2 more
exaly  

Long-term benefit of enzyme replacement therapy in Pompe disease

Neurology, 2017
E. Kuperus, M. Kruijshaar, S. Wens, J. D. de Vries, M. Favejee, J. C. van der Meijden, D. Rizopoulos, E. Brusse, Pieter A. Van Doorn, A. T. van der Ploeg, N. A. van der Beek   +10 more
semanticscholar   +1 more source

Hormone replacement therapy in the menopause: a pro opinion

Ca-A Cancer Journal for Clinicians, 1996
H O Smith
exaly  

Enzyme replacement therapy for Gaucher disease

Expert Opinion on Biological Therapy, 2009
Joel Charrow
exaly  

Lucerastat, an Iminosugar for Substrate Reduction Therapy: Tolerability, Pharmacodynamics, and Pharmacokinetics in Patients With Fabry Disease on Enzyme Replacement

Clinical pharmacology and therapy, 2018
N. Guérard, D. Oder, P. Nordbeck, C. Zwingelstein, O. Morand, R. Welford, J. Dingemanse, C. Wanner   +7 more
semanticscholar   +1 more source

Enzyme Replacement Therapy for Mucopolysaccharidoses: Opinions of Patients and Families

Journal of Pediatrics, 2008
David Coman, Martin Delatycki, J Ed Wraith   +2 more
exaly