Results 141 to 150 of about 5,752 (150)

Long-term outcomes of elosulfase alfa enzyme replacement therapy in adults with MPS IVA: a sub-analysis of the Morquio A Registry Study (MARS). [PDF]

Orphanet J Rare Dis
Stepien KM, Burton BK, Bober MB, Campeau PM, Ellaway C, Bhattacharya K, Guffon N, Hinds D, Hunt A, Lail A, Lin SP, Magner M, Murphy E, Reisewitz P, Mitchell JJ.   +14 more
europepmc   +1 more source

Commission des Communautes Europeennes: Groupe du Porte-Parole. Rendez-vous de midi du 29.3.1988 (C.D. Ehlermann) = Commission of European Communities: Spokesman Group. Appointment at Noon on 29.3.1988 (C.D. Ehlermann). Press Spokesman Service Note to National Offices Bio No. (88) 112, 29 March 1988 [PDF]

, 1988

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Mucopolysaccharidoses-What Clinicians Need to Know: A Clinical, Biochemical, and Molecular Overview. [PDF]

Biomolecules
Lipiński P, Różdżyńska-Świątkowska A, Wiśniewska K, Rusecka J, Ługowska A, Żuber Z, Jezela-Stanek A, Cyske Z, Gaffke L, Pierzynowska K, Węgrzyn G, Tylki-Szymańska A.   +11 more
europepmc   +1 more source

Nonviral delivery of nCas9 for "safe harbor" integration to treat MPS IVA. [PDF]

Mol Ther Methods Clin Dev
Ou L.
europepmc   +1 more source

Real-world treatment with elosulfase alfa in patients with MPS IVA is associated with improved endurance over time. [PDF]

Genet Med Open
Burton BK, Stepien KM, Campeau PM, Sutton J, Hunt A, Reisewitz P, Hinds D.   +6 more
europepmc   +1 more source

Identification of Surrogate Biomarkers for Mucopolysaccharidosis Type IVA. [PDF]

Int J Mol Sci
Ago Y, Khan S, Klipner K, Bradford A, Tomatsu S.   +4 more
europepmc   +1 more source

The effects of decomposing animal remains on cave invertebrate communities [PDF]

, 1997
MacDonald, J, Terrell-Nield, C
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KBG syndrome: report and follow-up on three unrelated patients observed at different ages. [PDF]

Ital J Pediatr
Serra G, Elefante P, Gazzitano Y, Memo L, Mineo V, Morando C, Nardello R, Piro E, Travan L, Corsello G.   +9 more
europepmc   +1 more source

The National Economic Accounts of the United States: Review, Appraisal, and Recommendations [PDF]

National Accounts Review Committee
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