Results 231 to 240 of about 49,324 (252)

A new hemophilia carrier nomenclature to define hemophilia in women and girls: Communication from the SSC of the ISTH

Journal of Thrombosis and Haemostasis, 2021
Karin P M Van Galen, Roseline d'Oiron, Peter A Kouides   +2 more
exaly  

Gene therapy for hemophilia: a review on clinical benefit, limitations, and remaining issues

Blood, 2021
Frank Leebeek
exaly  

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

Nature Medicine, 2006
Valder R Arruda, Margareth C Ozelo, Hiroyuki Nakai   +2 more
exaly  

Prophylaxis versus Episodic Treatment to Prevent Joint Disease in Boys with Severe Hemophilia

New England Journal of Medicine, 2007
Sharon Funk Dpt, Michael Recht, J Michael Soucie   +2 more
exaly  

An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia

Nature Medicine, 2015
Husain Attarwala, Stuart Milstein, Muthiah Manoharan   +2 more
exaly  

Safety and pharmacokinetics of anti‐TFPI antibody (concizumab) in healthy volunteers and patients with hemophilia: a randomized first human dose trial

Journal of Thrombosis and Haemostasis, 2015
P Chowdary
exaly  

Update on clinical gene therapy for hemophilia

Blood, 2019
Roland W Herzog, David M Markusic
exaly