ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane +43 more
wiley +1 more source
HEI Initiative Training Handbook
This Handbook describes the development and implementation of one training programme for students developed by UTAD during the spring of 2022 and implemented during the fall of the same year. The programme development was mainly based in the three HEI’s experience with entrepreneurship formal education and in a survey identifying students’ major ...
Kowalik, Wojciech +6 more
openaire +1 more source
ABSTRACT The Clinical Assessment Scale in Autoimmune Encephalitis (CASE) tracks disease severity in autoimmune encephalitis (AE), but no threshold for significant change exists. We aimed to determine the minimally clinically important difference (MCID) for CASE.
Yihui Goh +8 more
wiley +1 more source
The impact of introducing a videolaryngoscope in the initial training of laryngoscopy for undergraduate medical students: a simulation randomized trial. [PDF]
Malito ML +4 more
europepmc +1 more source
Protocol for the assessment of self-harm in young people: initial audit and training implications [PDF]
Sarah Huline‐Dickens, Tony Adiele
openalex +1 more source
Particularities of movement skills manifestation by young gymnasts at initial training stage
Djamshid Umarov
openalex +2 more sources
Von Economo Neuron Loss in Frontotemporal Dementia: A Meta‐Analysis of Neuropathological Studies
ABSTRACT Von Economo neurons (VENs) have been reported to be vulnerable to neurodegeneration in frontotemporal dementia (FTD), particularly the behavioral variant (bvFTD), but these findings have not been systematically assessed across independent brain banks.
Daniel Talmasov +2 more
wiley +1 more source
Pour une réforme des programmes de formation initiale des enseignants en Afrique de l’Ouest
Abdeljalil Akkari, Valérie Vinuesa
doaj +1 more source
Social Science Pedagogy as a Way of Integrating Sustainable Education and Global Citizenship into the Initial Training of Pre-Primary Teachers. [PDF]
Diez R +3 more
europepmc +1 more source
A Systematic Comparison of Alpha‐Synuclein Seed Amplification Assays for Increasing Reproducibility
ABSTRACT Seed amplification assays (SAAs) enable ultrasensitive detection of misfolded α‐synuclein across biofluids and tissues. Yet, heterogeneity in protocols limits cross‐study comparability and clinical translation. Here, we review α‐synuclein SAA methods and their performance across various biological matrices.
Manuela Amaral‐do‐Nascimento +3 more
wiley +1 more source

