In-silico pharmacological insights into the therapeutic potential of microRNAs for microplastic-associated cancers. [PDF]
Baspakova A +11 more
europepmc +1 more source
Mesenchymal Stem Cell-Derived Extracellular Vesicles: Seeking into Cell-Free Therapies for Bone-Affected Lysosomal Storage Disorders. [PDF]
Leal AF, Pachajoa H, Tomatsu S.
europepmc +1 more source
CRISPR/Cas-Based Ex Vivo Gene Therapy and Lysosomal Storage Disorders: A Perspective Beyond Cas9. [PDF]
Leal AF, Prieto LE, Pachajoa H.
europepmc +1 more source
A Rare Compound Heterozygous NAGLU Gene Mutation in Two Siblings with Mucopolysaccharidosis type Iiib. [PDF]
Vahedi-Larijani L +5 more
europepmc +1 more source
Neuraminidase 1 secondary deficiency contributes to CNS pathology in neurological mucopolysaccharidoses via brain protein hypersialylation. [PDF]
Xu T +23 more
europepmc +1 more source
Evaluation of AAV vectors with tissue-specific or ubiquitous promoters in a mouse model of mucopolysaccharidosis type IVA. [PDF]
Khan SA +4 more
europepmc +1 more source
Radiographic assessment of mucopolysaccharidoses: A pictorial review. [PDF]
Teixeira de Castro Gonçalves Ortega AC +2 more
europepmc +1 more source
Hearing loss in patients with Morquio A syndrome: A scoping review. [PDF]
Diaz-Ordoñez L +8 more
europepmc +1 more source

