Results 381 to 390 of about 342,419 (394)

Spinal muscular atrophy — insights and challenges in the treatment era

Nature Reviews Neurology, 2020
Eugenio Mercuri, Maria Carmela Pera, Richard S Finkel   +2 more
exaly  

Muscular Dystrophies

Pediatric Annals, 2005
openaire   +2 more sources

Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy

Nature Medicine, 2020
exaly  

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly  

Dysregulation of calcium homeostasis in muscular dystrophies

Expert Reviews in Molecular Medicine, 2014
A. Vallejo-Illarramendi, I. Toral-Ojeda, G. Aldanondo, A. López de Munain   +3 more
semanticscholar   +1 more source

Advances in therapy for spinal muscular atrophy: promises and challenges

Nature Reviews Neurology, 2018
Ewout J N Groen, Kevin Talbot, Thomas Gillingwater   +2 more
exaly  

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

Lancet Neurology, The, 2010
David J Birnkrant, Laura E. Case, Paula R Clemens   +2 more
exaly  

Duchenne and Becker muscular dystrophies.

Neurologic clinics, 2014
K. Flanigan
semanticscholar   +1 more source

Short Telomeres and Stem Cell Exhaustion Model Duchenne Muscular Dystrophy in mdx/mTR Mice

Cell, 2010
Alessandra Sacco, Foteini Mourkioti, Scott L Delp   +2 more
exaly  

Muscular Dystrophies

2001
openaire   +2 more sources