Results 141 to 150 of about 60,007 (250)

Ataluren for the treatment of people living with nonsense mutation Duchenne muscular dystrophy: a plain language summary of Study 041. [PDF]

J Comp Eff Res
Wu S, Vlodavets D, de Queiroz Campos Araujo AP, Castle J.   +3 more
europepmc   +1 more source

Survey of Adrenal Insufficiency Management for Duchenne muscular dystrophy in Italy. [PDF]

Endocrine
Tornese G, Wong SC, Sbrocchi AM, De Angelis F, Zito I, Weber DR, Aversa T.   +6 more
europepmc   +1 more source

Early Cardiac Manifestations as the Initial Presentation of Duchenne Muscular Dystrophy in Infancy. [PDF]

Cureus
Shatarat F, Alkasasbeh J, Shatarat R, Tarawneh S.   +3 more
europepmc   +1 more source

Management of adrenal insufficiency risk after long-term systemic glucocorticoid therapy in Duchenne muscular dystrophy: Clinical practice recommendations [PDF]

, 2019
Bowden, Sasigarn A, Connolly, Anne M, Kinnett, Kathi, Zeitler, Philip S   +3 more
core   +1 more source

Exosome-Mediated Benefits of Cell Therapy in Mouse and Human Models of Duchenne Muscular Dystrophy. [PDF]

Stem Cell Reports
Aminzadeh MA, Rogers RG, Fournier M, Tobin RE, Guan X, Childers MK, Andres AM, Taylor DJ, Ibrahim A, Ding X, Torrente A, Goldhaber JM, Lewis M, Gottlieb RA, Victor RA, Marbán E.   +15 more
europepmc   +1 more source

An Assessment of Paediatricians' Knowledge and Perspectives of Duchenne Muscular Dystrophy in Oman. [PDF]

Sultan Qaboos Univ Med J
Al Jabri Z, Alsawaie M, Saki Malehi A, Al Futaisi A, Al-Amrani F.   +4 more
europepmc   +1 more source

Duchenne Muscular Dystrophy: Contemporary Therapeutic Options and Real-World Challenges in Treatment Selection. [PDF]

Muscles
Pesco MT, Öztürk GZ, Bhadola SC, Chrzanowski SM, Gushchina LV, D'Ambrosio ES.   +5 more
europepmc   +1 more source

State-of-the-Art Research and New Pharmacological Perspectives on Renal Involvement in Duchenne Muscular Dystrophy: A Narrative Review. [PDF]

Biomedicines
Bellis M, Imbrici P, Lenti R, Liantonio A, De Luca A.   +4 more
europepmc   +1 more source

Clinico-genetic heterogeneity in Pakistani families affected with muscular dystrophies. [PDF]

Mol Biol Rep
Ahmad R, Hashmi MA, Ullah A, Rehman UU, Naeem M, Houlden H.   +5 more
europepmc   +1 more source

Neonatal screening for Duchenne muscular dystrophy in eastern China: a closed prospective study. [PDF]

Transl Pediatr
Qian G, Yang R, Huang X, Wu D, Fang K, Zhao Z.   +5 more
europepmc   +1 more source