Results 221 to 228 of about 75,574 (228)

Duchenne Muscular Dystrophy

2005
Erynn S. Gordon, Eric P. Hoffman
openaire   +1 more source

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly  

Adenine base editing in mouse embryos and an adult mouse model of Duchenne muscular dystrophy

Nature Biotechnology, 2018
Seuk-Min Ryu, T. Koo, Kyoungmi Kim, Kayeong Lim, Gayoung Baek, Sang-Tae Kim, H. Kim, Daesik Kim, Hyunji Lee, Eugene Chung, Jin-Soo Kim   +10 more
semanticscholar   +1 more source

Advances in therapy for spinal muscular atrophy: promises and challenges

Nature Reviews Neurology, 2018
Ewout J N Groen, Kevin Talbot, Thomas Gillingwater   +2 more
exaly  

A mutation-independent approach for muscular dystrophy via upregulation of a modifier gene

Nature, 2019
Dwi U Kemaladewi, Steven Erwood, Steven A Prescott   +2 more
exaly  

Deletion of brain dystroglycan recapitulates aspects of congenital muscular dystrophy

Nature, 2002
Steven A Moore, Michael D Henry, Kevin P Campbell   +2 more
exaly  

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

Lancet Neurology, The, 2010
David J Birnkrant, Laura E. Case, Paula R Clemens   +2 more
exaly  

Short Telomeres and Stem Cell Exhaustion Model Duchenne Muscular Dystrophy in mdx/mTR Mice

Cell, 2010
Alessandra Sacco, Foteini Mourkioti, Scott L Delp   +2 more
exaly