Results 281 to 290 of about 106,524 (297)

Carnitine in duchenne muscular dystrophy

Clinica Chimica Acta, 1979
Mawatari Shiro, Kobayashi Takuro, Shinnoh Nobue   +2 more
openaire   +3 more sources

Induced pluripotent stem cells from a spinal muscular atrophy patient

Nature, 2008
Allison D Ebert, Christian L Lorson, Clive N Svendsen   +2 more
exaly  

Adenine base editing in mouse embryos and an adult mouse model of Duchenne muscular dystrophy

Nature Biotechnology, 2018
Seuk-Min Ryu, T. Koo, Kyoungmi Kim, Kayeong Lim, Gayoung Baek, Sang-Tae Kim, H. Kim, Daesik Kim, Hyunji Lee, Eugene Chung, Jin-Soo Kim   +10 more
semanticscholar   +1 more source

Steroids in Duchenne muscular dystrophy

Neuromuscular Disorders, 2013
Valeria Ricotti, Deborah Ridout, Francesco Muntoni   +2 more
openaire   +3 more sources

Defective membrane repair in dysferlin-deficient muscular dystrophy

Nature, 2003
Steven S Vogel, Chien-Chang Chen, Kevin P Campbell   +2 more
exaly  

Genetic and pharmacologic inhibition of mitochondrial-dependent necrosis attenuates muscular dystrophy

Nature Medicine, 2008
Douglas P Millay, Christopher P Baines, Elisabeth R Barton   +2 more
exaly  

Spinal muscular atrophy — insights and challenges in the treatment era

Nature Reviews Neurology, 2020
Eugenio Mercuri, Maria Carmela Pera, Richard S Finkel   +2 more
exaly  

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly  

Advances in therapy for spinal muscular atrophy: promises and challenges

Nature Reviews Neurology, 2018
Ewout J N Groen, Kevin Talbot, Thomas Gillingwater   +2 more
exaly  

Duchenne Muscular Dystrophy

2019
Charles V. Pollack, Richard M. Cantor, Victoria G. Riese   +2 more
openaire   +2 more sources