Results 201 to 210 of about 7,021 (220)

Therapeutic approaches for Duchenne muscular dystrophy

Nature Reviews Drug Discovery, 2023
Thomas C Roberts, Kay E Davies
exaly  

Spinal muscular atrophy

Nature Reviews Disease Primers, 2022
Francesco Muntoni, Richard S Finkel
exaly  

Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

Nature Medicine, 2019
Christopher E Nelson, Yaoying Wu, Matthew A Waller   +2 more
exaly  

Induced pluripotent stem cells from a spinal muscular atrophy patient

Nature, 2008
Allison D Ebert, Christian L Lorson, Clive N Svendsen   +2 more
exaly  

Diagnostic criteria for facioscapulohumeral muscular dystrophy

Neuromuscular Disorders, 1991
P.W. Lunt, G.W. Padberg, Michel Fardeau, M. Koch   +3 more
openaire   +3 more sources

Therapeutic developments for Duchenne muscular dystrophy

Nature Reviews Neurology, 2019
Ingrid E C Verhaart, Annemieke Aartsma-Rus   +1 more
exaly  

Detection of collagens by multispectral optoacoustic tomography as an imaging biomarker for Duchenne muscular dystrophy

Nature Medicine, 2019
Adrian P Regensburger, Jörg Jüngert, Teresa Gerhalter   +2 more
exaly  

Defective membrane repair in dysferlin-deficient muscular dystrophy

Nature, 2003
Steven S Vogel, Chien-Chang Chen, Kevin P Campbell   +2 more
exaly  

Genetic and pharmacologic inhibition of mitochondrial-dependent necrosis attenuates muscular dystrophy

Nature Medicine, 2008
Douglas P Millay, Christopher P Baines, Elisabeth R Barton   +2 more
exaly  

Spinal muscular atrophy — insights and challenges in the treatment era

Nature Reviews Neurology, 2020
Eugenio Mercuri, Maria Carmela Pera, Richard S Finkel   +2 more
exaly