Results 211 to 220 of about 7,021 (220)

Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy

Nature Medicine, 2020
exaly  

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly  

Advances in therapy for spinal muscular atrophy: promises and challenges

Nature Reviews Neurology, 2018
Ewout J N Groen, Kevin Talbot, Thomas Gillingwater   +2 more
exaly  

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

Lancet Neurology, The, 2010
David J Birnkrant, Laura E. Case, Paula R Clemens   +2 more
exaly  

Short Telomeres and Stem Cell Exhaustion Model Duchenne Muscular Dystrophy in mdx/mTR Mice

Cell, 2010
Alessandra Sacco, Foteini Mourkioti, Scott L Delp   +2 more
exaly  

Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management

Lancet Neurology, The, 2018
David J Birnkrant, Carla M Bann, Benjamin A Alman   +2 more
exaly  

A mutation-independent approach for muscular dystrophy via upregulation of a modifier gene

Nature, 2019
Dwi U Kemaladewi, Steven Erwood, Steven A Prescott   +2 more
exaly  

Ultrarare Muscular Dystrophy Mimics Facioscapulohumeral Muscular Dystrophy

Pediatric Neurology
Bret J. Gardner, Meeta Cardon
openaire   +2 more sources

Deletion of brain dystroglycan recapitulates aspects of congenital muscular dystrophy

Nature, 2002
Steven A Moore, Michael D Henry, Kevin P Campbell   +2 more
exaly  

Infantile facioscapulohumeral muscular dystrophy

Pediatric Neurology, 1992
Oebele F. Brouwer, George W. Padberg
openaire   +2 more sources