Results 251 to 260 of about 104,787 (267)

Muscular Dystrophies

2001
openaire   +2 more sources

Induced pluripotent stem cells from a spinal muscular atrophy patient

Nature, 2008
Allison D Ebert, Christian L Lorson, Clive N Svendsen   +2 more
exaly  

Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

Nature Medicine, 2019
Christopher E Nelson, Yaoying Wu, Matthew A Waller   +2 more
exaly  

Defective membrane repair in dysferlin-deficient muscular dystrophy

Nature, 2003
Steven S Vogel, Chien-Chang Chen, Kevin P Campbell   +2 more
exaly  

Therapeutic developments for Duchenne muscular dystrophy

Nature Reviews Neurology, 2019
Ingrid E C Verhaart, Annemieke Aartsma-Rus   +1 more
exaly  

Detection of collagens by multispectral optoacoustic tomography as an imaging biomarker for Duchenne muscular dystrophy

Nature Medicine, 2019
Adrian P Regensburger, Jörg Jüngert, Teresa Gerhalter   +2 more
exaly  

Genetic and pharmacologic inhibition of mitochondrial-dependent necrosis attenuates muscular dystrophy

Nature Medicine, 2008
Douglas P Millay, Christopher P Baines, Elisabeth R Barton   +2 more
exaly  

Spinal muscular atrophy — insights and challenges in the treatment era

Nature Reviews Neurology, 2020
Eugenio Mercuri, Maria Carmela Pera, Richard S Finkel   +2 more
exaly  

Ultrarare Muscular Dystrophy Mimics Facioscapulohumeral Muscular Dystrophy

Pediatric Neurology
Bret J. Gardner, Meeta Cardon
openaire   +2 more sources

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly