Results 251 to 260 of about 362,296 (275)

Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy

Nature Medicine, 2020
Alessandra Moretti, Daniel Sinnecker, Shicheng Sun   +2 more
exaly  

Muscular dystrophies

Disease-a-Month, 1972
openaire   +2 more sources

Eteplirsen treatment for Duchenne muscular dystrophy

Neurology, 2018
J. Charleston, F. Schnell, J. Dworzak, C. Donoghue, S. Lewis, Lei Chen, Gavin Young, A. Milici, J. Voss, U. deAlwis, B. Wentworth, L. Rodino-Klapac, Z. Sahenk, D. Frank, J. Mendell   +14 more
semanticscholar   +1 more source

Muscular Dystrophies

Pediatric Annals, 2005
openaire   +2 more sources

Advances in Muscular Dystrophies

JAMA Neurology, 2015
Peter B, Kang, Robert C, Griggs
openaire   +2 more sources

Muscular Dystrophies

1984
Michael Swash, Martin S. Schwartz
openaire   +1 more source

Induced pluripotent stem cells from a spinal muscular atrophy patient

Nature, 2008
Allison D Ebert, Christian L Lorson, Clive N Svendsen   +2 more
exaly  

Muscular Dystrophies

2001
openaire   +2 more sources

Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

Nature Medicine, 2019
Christopher E Nelson, Yaoying Wu, Matthew A Waller   +2 more
exaly  

Defective membrane repair in dysferlin-deficient muscular dystrophy

Nature, 2003
Steven S Vogel, Chien-Chang Chen, Kevin P Campbell   +2 more
exaly