Results 261 to 270 of about 362,296 (275)

Genetic and pharmacologic inhibition of mitochondrial-dependent necrosis attenuates muscular dystrophy

Nature Medicine, 2008
Douglas P Millay, Christopher P Baines, Elisabeth R Barton   +2 more
exaly  

Spinal muscular atrophy — insights and challenges in the treatment era

Nature Reviews Neurology, 2020
Eugenio Mercuri, Maria Carmela Pera, Richard S Finkel   +2 more
exaly  

Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy

Nature Medicine, 2002
Scott Q Harper, Dongsheng Duan, John F Engelhardt   +2 more
exaly  

Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management

Lancet Neurology, The, 2018
David J Birnkrant, Carla M Bann, Benjamin A Alman   +2 more
exaly  

Advances in therapy for spinal muscular atrophy: promises and challenges

Nature Reviews Neurology, 2018
Ewout J N Groen, Kevin Talbot, Thomas Gillingwater   +2 more
exaly  

Congenital Muscular Dystrophy

Pediatric Annals, 2005
Eugenio, Mercuri, Cheryl, Longman
openaire   +2 more sources

A mutation-independent approach for muscular dystrophy via upregulation of a modifier gene

Nature, 2019
Dwi U Kemaladewi, Steven Erwood, Steven A Prescott   +2 more
exaly  

Deletion of brain dystroglycan recapitulates aspects of congenital muscular dystrophy

Nature, 2002
Steven A Moore, Michael D Henry, Kevin P Campbell   +2 more
exaly  

Ultrarare Muscular Dystrophy Mimics Facioscapulohumeral Muscular Dystrophy

Pediatric Neurology
Bret J. Gardner, Meeta Cardon
openaire   +2 more sources

Muscular Dystrophies of Childhood

Pediatric Annals, 1977
G E, Slater, K F, Swaiman
openaire   +2 more sources