Contribution of neuromuscular Impairment to physical functional Status in Patients with Lumbar Spinal Stenosis [PDF]
Fossel, Anne H. +4 more
core
Enhanced Vatiquinone Bioavailability With Fatty Meals and Optimal Dosing Schedule
This investigation discusses two clinical studies. One investigated the effect of fatty meals (≥ 25% fat) on vatiquinone PK exposures, and the other one characterized vatiquinone PK profiles when administered on a TID dosing regimen corresponding to mealtimes. The data support the recommendation of administering vatiquinone with fatty meals (≥ 25% fat)
Lucy Lee +6 more
wiley +1 more source
Therapeutic targeting of RNA for neurological and neuromuscular disease. [PDF]
Bubenik JL, Scotti MM, Swanson MS.
europepmc +1 more source
Current Treatment of Neuromuscular Diseases
Lisa Kokontis, Ludwig Gutmann
openalex +1 more source
ABSTRACT To enable adeno‐associated viral vectors (AAV) to achieve their maximum potential, next‐generation manufacturing processes must be developed to make gene therapies more affordable and accessible. This study focused on the design of two different intensified AAV downstream manufacturing processes at bench and pilot scale.
Akshay S. Chaubal +6 more
wiley +1 more source
The impact of respiratory muscle training on respiratory function in patients with neuromuscular disease: a systematic review and meta-analysis of randomized controlled trials. [PDF]
Ortiz-Garcia NY +12 more
europepmc +1 more source
Pressure Support Versus Assisted Controlled Noninvasive Ventilation in Neuromuscular Disease [PDF]
Karim Chadda +5 more
openalex +1 more source
Respiratory Implications of Pediatric Neuromuscular Disease
H. Panitch
semanticscholar +1 more source
Extracellular vesicles (EVs) derived from stem cells show promise for applications in regenerative medicine, but their scalability and yield remain challenges. This review explores the approaches for biophysical modulations within cell niches on EV properties, discusses the current clinical application of EVs, and provides an outlook on the existing ...
Yang Xu +9 more
wiley +1 more source
TRPV4 neuromuscular disease registry highlights bulbar, skeletal and proximal limb manifestations. [PDF]
Kosmanopoulos GP +20 more
europepmc +1 more source

