Results 161 to 170 of about 6,859 (228)

Nusinersen for children with type I spinal muscular atrophy: 4 years’ clinical experience in Turkish cohort [PDF]

Ömer Bektaş, Murat Gülşen, Onur Burak Dursun, Ahmet Tekin, Deniz Yüksel, Ercan Demir, Gülten Öztürk, Sema Saltık, Özlem Hergüler, Ayşe Aysima Özçelik, Hüseyin Tan, Bilge Özgör, Arzu Ekici, Merve Feyza Yüksel, Süleyman Şahin, Özgür Duman, Mustafa Kömür, Figen Baydan, Edibe Pembegül Yıldız, Bülent Kara, Uluç Yiş, Seda Kanmaz, Kürşat Bora Çarman, Elif Acar Arslan, Mehmet Canpolat, Ahmet Sami Güven, Gökçen Öz-Tuncer, Aycan Ünalp, Didem Ardıçlı, Aynur Ayşe Karaduman, Gökmen Zararsız, Gülhıs Deda, Turkish SMA Study Group   +32 more
openalex   +1 more source

Evaluating the Effects of Nusinersen Treatment in Adults With Spinal Muscular Atrophy Using Axonal Excitability and MscanFit MUNE. [PDF]

Muscle Nerve
Alaamel A, Erdem NŞ, Gencer GYG, Kaya HC, Uysal H.   +4 more
europepmc   +1 more source

Transforming Spinal Muscular Atrophy: From Pivotal Trials to Real-World Evidence and Future Therapeutic Frontiers in Types 1 and 2. [PDF]

Biomedicines
Belančić A, Eustaquio PC, Gkrinia EMM, Rački V, Pilipović K, Vitezić D.   +5 more
europepmc   +1 more source

CT-guided Lumbar Puncture for Intrathecal Nusinersen Injection in Patients with Spinal Muscular Atrophy: Technical Effectiveness, Safety, and Radiation Dose [PDF]

Yannick Laurent Thal, Marcel Optiz, Raya Serger, Laura Kluener, Daniel Rosok, M Drews, Denise Bos, Johannes Haubold, Christoph Kleinschnitz, Tim Hagenacker, Michael Forsting, Cornelius Deuschl, Zensen Sebastian   +12 more
openalex   +1 more source

Spontaan spinaal epiduraal hematoom bij acute rugpijn [PDF]

, 2017
Anisau, Aliaksandr, Vangeneugden, Johan, Vanhoenacker, Filip   +2 more
core   +1 more source

Pioneering SMA therapies for all types: survival gains, cost dynamics, and performance-based agreements. [PDF]

Cost Eff Resour Alloc
Al-Jedai A, Al-Mudaiheem H, AlSakran A, Bashiri FA, Ghamdi F, Almuhaizea MA, AlSamman A, Awad N, Ojeil R.   +8 more
europepmc   +1 more source

O USO DO NUSINERSEN NO TRATAMENTO DA ATROFIA MUSCULAR ESPINHAL: REVISÃO DE LITERATURA

, 2020
Elzanice Monteiro DOMINGOS, Annalu Moreira Aguiar   +1 more
openalex   +2 more sources

Advancing personalized spinal muscular atrophy care: matching the right biomarker to the right patient at the right time. [PDF]

J Neurol
Corti S, Ottoboni L, Sansone V.
europepmc   +1 more source

Respiratory Outcomes of Spinal Muscular Atrophy Patients Receiving Nusinersen in Hong Kong

Jacqueline Hung, Ka Ka Siu, Shuk Kuen Chau, So Lun Lee, H.S. Chan   +4 more
openalex   +1 more source

Respiratory function in 192 adult patients with spinal muscular atrophy (SMA) treated with nusinersen - a multicenter observational study. [PDF]

Orphanet J Rare Dis
Wurster CD, Stolte B, Kessler T, Freigang M, Bjelica B, Ilse B, Koch JC, Cordts I, Mensch A, Zeller D, Uzelac Z, Sam G, Lapp HS, Wohnrade C, Rödiger A, Muhandes MT, Schneider I, Bellut J, Nentwich J, Dorst J, Schuster J, Schreiber-Katz O, Osmanovic A, Totzeck A, Thimm A, Steinbach R, Grosskreutz J, Kleinschnitz C, Ludolph AC, Deschauer M, Kirschner J, Dreyhaupt J, Wollinsky K, Petri S, Weiler M, Hagenacker T, Günther R.   +36 more
europepmc   +1 more source