Results 181 to 190 of about 6,546 (245)

Comparative Clinical Outcomes of Nusinersen and Gene Therapy in Spinal Muscular Atrophy Type 1.

JAMA Netw Open
Ropars J, Cances C, Garcia-Uzquiano R, Gomez-Garcia de la Banda M, Barnerias C, Audic F, Durigneux J, Halbert C, Nkam L, Laugel V, Espil C, Walther-Louvier U, Davion JB, Isapof A, Le Goff L, Desguerre I, Quijano-Roy S, Grimaldi L, French SMA Registry Study Group.   +18 more
europepmc   +1 more source

Evaluating Therapeutic Outcomes in Spinal Muscular Atrophy: An Indian Experience. [PDF]

Ann Indian Acad Neurol
Mohanlal S, Mubeena PM, Hussain H, Anand M, Kumar S, Ashraf VV, Rabia TA, Janardhanan S, Kumar S.   +8 more
europepmc   +1 more source

Systematic Review and Meta-analysis of Long-Term Nusinersen Effectiveness in Adolescents and Adults with Spinal Muscular Atrophy. [PDF]

Adv Ther
Hagenacker T, Paradis AD, Lawson-Michod KA, Youn B.   +3 more
europepmc   +1 more source

Biomarkers in spinal muscular atrophy. [PDF]

Front Neurol
Yan L, Zhang J, Zheng J, Hao H.
europepmc   +1 more source

Spontaan spinaal epiduraal hematoom bij acute rugpijn [PDF]

, 2017
Anisau, Aliaksandr, Vangeneugden, Johan, Vanhoenacker, Filip   +2 more
core   +1 more source

Quebec Spinal Muscular Atrophy Newborn Screening Program: The First Year Experience. [PDF]

Int J Neonatal Screen
Groulx-Boivin E, Belzile A, Nguyen CÉ, Gauthier A, Chrestian N, Michaud-Gosselin C, Giguère Y, Berthier MT, Soucy JF, Laberge AM, Oskoui M.   +10 more
europepmc   +1 more source

Managing Spinal Muscular Atrophy: A Look at the Biology and Treatment Strategies. [PDF]

Biology (Basel)
Vezzoli A, Bottai D, Adami R.
europepmc   +1 more source

Surgical Access for Intrathecal Therapy in Spinal Muscular Atrophy with Spinal Fusion: Long-Term Outcomes of Lumbar Laminectomy. [PDF]

J Clin Med
Potaczek T, Duda S, Adamczyk J.
europepmc   +1 more source

Post-Marketing Safety of Spinal Muscular Atrophy Therapies: Analysis of Spontaneous Adverse Drug Reactions from EudraVigilance. [PDF]

J Clin Med
Belančić A, Mas P, Miletić L, Kovačić Bytyqi B, Vitezić D.   +4 more
europepmc   +1 more source

Single Nucleotide <i>SMN1</i> Variants in a Cohort of Individuals With Spinal Muscular Atrophy. [PDF]

Neurol Genet
Rimoldi M, Magri F, Meneri M, Gagliardi D, Ada Sansone V, Albamonte E, Ottoboni L, Comi GP, Mercuri E, Tiziano FD, Ronchi D, Corti S.   +11 more
europepmc   +1 more source