Results 191 to 200 of about 6,859 (228)

Performance fatigability in adults with spinal muscular atrophy treated long‐term with nusinersen [PDF]

Benjamin Stolte, Svenja Neuhoff, Jaqueline Lipka, Melina Schlag, Otgonzul von Velsen, Teresa Kruse, Cornelius Deuschl, Christoph Kleinschnitz, Tim Hagenacker   +8 more
openalex   +1 more source

Systematic Review and Meta-analysis of Long-Term Nusinersen Effectiveness in Adolescents and Adults with Spinal Muscular Atrophy. [PDF]

Adv Ther
Hagenacker T, Paradis AD, Lawson-Michod KA, Youn B.   +3 more
europepmc   +1 more source

Biomarkers in spinal muscular atrophy. [PDF]

Front Neurol
Yan L, Zhang J, Zheng J, Hao H.
europepmc   +1 more source

Extracellular Matrix Remodeling in Motor Neuron Diseases. [PDF]

Int J Mol Sci
Apolloni S, Tortoriello S, Milani M, Rossi S.   +3 more
europepmc   +1 more source

Machine learning predicts treatment response to nusinersen in non-sitter Spinal Muscular Atrophy (SMA).

Stimpson G, O'Reilly E, Coratti G, Ridout D, Chakraborti T, Mitra R, de Sanctis R, Pane M, Scoto M, Mercuri E, Muntoni F, Baranello G, International SMA Consortium.   +12 more
europepmc   +1 more source

Quebec Spinal Muscular Atrophy Newborn Screening Program: The First Year Experience. [PDF]

Int J Neonatal Screen
Groulx-Boivin E, Belzile A, Nguyen CÉ, Gauthier A, Chrestian N, Michaud-Gosselin C, Giguère Y, Berthier MT, Soucy JF, Laberge AM, Oskoui M.   +10 more
europepmc   +1 more source

Longitudinal evaluation of fatigue in adult patients with spinal muscular atrophy and the impact of disease-modifying drugs. [PDF]

Arq Neuropsiquiatr
Graça FFD, Iwabe C, França MC.
europepmc   +1 more source

Managing Spinal Muscular Atrophy: A Look at the Biology and Treatment Strategies. [PDF]

Biology (Basel)
Vezzoli A, Bottai D, Adami R.
europepmc   +1 more source

Surgical Access for Intrathecal Therapy in Spinal Muscular Atrophy with Spinal Fusion: Long-Term Outcomes of Lumbar Laminectomy. [PDF]

J Clin Med
Potaczek T, Duda S, Adamczyk J.
europepmc   +1 more source

Post-Marketing Safety of Spinal Muscular Atrophy Therapies: Analysis of Spontaneous Adverse Drug Reactions from EudraVigilance. [PDF]

J Clin Med
Belančić A, Mas P, Miletić L, Kovačić Bytyqi B, Vitezić D.   +4 more
europepmc   +1 more source