Results 61 to 70 of about 166,938 (112)

Olipudase alfa for the treatment of acid sphingomyelinase deficiency (ASMD): safety and efficacy in adults treated for 30months [PDF]

Molecular Genetics and Metabolism, 2017
Ana Cristina Puga, Melissa Wasserstein, George Diaz, Robin Lachmann, Marie-Helene Jouvin, Indrani Nandy, Allena Ji, Haig Ingulizian   +7 more
openaire   +1 more source

Alfa Card

Card for Alfa, a hotel, restaurant, and garage.
Alfa Hotel
core  

Alfa-Cakes-Fabrik G.m.b.H, Radebeul-Dresden, Befreiungshalle.

ALFA-CAKES-FABRIK G.M.B.H, RADEBEUL-DRESDEN, BEFREIUNGSHALLE. Alfa-Cakes-Fabrik G.m.b.H, Radebeul-Dresden, Befreiungshalle. ( -
Alfa-Cakes-Fabrik G.m.b.H.
core   +1 more source

Apresentação

, 2001
Alfa, Revista
core   +4 more sources

O33: Impact of p.Arg610del neuroprotective genotype on disease burden and treatment response in adults with acid-sphingomyelinase deficiency: ASCEND olipudase alfa trial

Genetics in Medicine Open
Melissa Wasserstein, Monica Kumar, Nicole Armstrong, Sefika Uslu Cil, Arya Firoozan, Lisa Underhill, Robin Lachmann   +6 more
doaj   +1 more source

P206: Continued clinical improvements in adults with acid sphingomyelinase deficiency after 3-5 Years of olipudase alfa treatment: Final ASCEND trial results

Genetics in Medicine Open
Melissa Wasserstein, Renata Gallagher, Antonio Barbato, Roberto Giugliani, Norberto Guelbert, Julia Hennermann, Takayuki Ikezoe, Robin Lachmann, Olivier Lidove, Paulina Mabe, Eugen Mengel, Maurizio Scarpa, Ebubekir Senates, Michel Tchan, Jesus Villarrubia, Beth Thurberg, Nicole Armstrong, Shruti Srivastava, Urszula Wisniewska, Monica Kumar   +19 more
doaj   +1 more source

P034: A real-world evidence study into the usage of olipudase alfa for acid sphingomyelinase deficiency in the United States

Genetics in Medicine Open
Judy Hull, Neeraj Rawat, Laurence Pollissard, Gavin Harper, Joe Conyers, Rabiyah Sahar   +5 more
openaire   +1 more source

Screening for acid sphingomyelinase deficiency in patients with an interstitial lung disease. [PDF]

Orphanet J Rare Dis
Vermant M, Van Raemdonck I, Veyt N, Carlon MS, Cortesi EE, De Crem N, De Rooy M, Follet T, Gogaert S, Vanaudenaerde B, Cassiman D, De Sadeleer LJ, Wuyts WA.   +12 more
europepmc   +1 more source

1973. Domenico Rea a Alfa Romeo - Alfa sud

, 1973
Rea, Domenico, Alfa Romeo - Alfasud
core   +1 more source

Patient Perspective-Where Does the Value for Money of a Treatment Really Lie? [PDF]

J Inherit Metab Dis
Mathieson TA, Evans WRH, Hopkin JL, Cowie SL.   +3 more
europepmc   +1 more source