Results 121 to 130 of about 270,959 (189)

Orphan and de novo Genes in Fungi and Animals: Identification, Origins and Functions. [PDF]

Genome Biol Evol
Seçkin E, Colinet D, Sarti E, Danchin EGJ.   +3 more
europepmc   +1 more source

Informing Dose for Pediatric Rare Diseases-A Survey of Recent Orphan Drugs Approvals. [PDF]

Clin Transl Sci
Fletcher EP, Kim C, Mei H, AbuAsal B, Samuels S, Madabushi R, Ramamoorthy A.   +6 more
europepmc   +1 more source

Strategic Drivers Behind Early Withdrawal of Orphan Designations in the EU: A Retrospective Analysis (2000-2024). [PDF]

Ther Innov Regul Sci
Bouwman L, Castanheira M, Siotis G.
europepmc   +1 more source

Machine learning can distinguish orphans that have resulted from sequence divergence beyond recognition. [PDF]

Bioinform Adv
Tassios E, de Leuw J, Nikolaou C, Kupczok A, Vakirlis N.   +4 more
europepmc   +1 more source

Drugs anticipated to be selected for Medicare price negotiation in 2026 for implementation in 2028. [PDF]

J Manag Care Spec Pharm
Cousin EM, Martin K, Hansen RN, Coster J, Sullivan SD.   +4 more
europepmc   +1 more source

Epidemiology, Treatment Patterns, and Cost Analysis of Immune Thrombocytopenia in Spain between 2014 and 2020: A Population-based Study

TH Open
Tomás J. González-López, Gabriela Alperovich, Elena Burillo, Marta Espejo-Saavedra Soler, Elena Rebollo-Gómez, Ignacio Hernández, Jose L. Justicia, María L. Lozano   +7 more
doaj   +1 more source

The Prevalence and Diversity of Marine Toxin-Antitoxin Systems. [PDF]

Mar Drugs
Liu C, Guo Y, Gu J, Wei Z, Chen P, Wang X.   +5 more
europepmc   +1 more source

Early and accelerated access programs for medical devices in the European Union: mapping regulatory derogations and national schemes. [PDF]

Front Med Technol
Haon B, Hartmann M, Akodad S, Stevens H, Rochaix L.   +4 more
europepmc   +1 more source

Advancing hypoparathyroidism treatment: FDA approval of Palopegteriparatide as a promising orphan drug. [PDF]

Ann Med Surg (Lond)
Shahid SR, Shahid K, Ehsan S, Khalid M, Waafira A.   +4 more
europepmc   +1 more source