Evolving Research and Development Landscape for Rare Diseases: Growing Concerns Over Orphan Drug Lag in Japan. [PDF]
Enya K+5 more
europepmc +1 more source
BL3 A CONCEPTUAL MODEL FOR POMPE DISEASE:THE BACKBONE FOR AN ECONOMIC EVALUATION OF AN ORPHAN DRUG
TA Kanters+5 more
openalex +1 more source
The challenge of accessing orphan drugs in the Middle East: A critical review [PDF]
Ziyad S. Almalki+3 more
openalex +1 more source
Genetic variation among progeny shapes symbiosis in a basidiomycete with poplar
Summary Forest trees rely on ectomycorrhizal (ECM) fungi for acquiring scarce resources such as water and nutrients. However, the molecular mechanisms governing ECM traits remain inadequately understood, particularly the role of intraspecific fungal variation in root‐tip colonisation and trophic interactions.
Benjamin Dauphin+9 more
wiley +1 more source
Weight Loss‐Associated Remodeling of Adipose Tissue Immunometabolism
ABSTRACT Obesity is a multifactorial condition characterized by excessive adiposity and systemic chronic low‐grade inflammation. Recent literature reflects a growing appreciation for the complex interplay between metabolism and the immune system in the pathogenesis of obesity‐related health conditions.
Paulo José Basso+5 more
wiley +1 more source
PHP100 EVALUATION OF ACCEPTANCE AND REJECTION RATES OF ORPHAN DRUGS ACROSS SIX HTA AGENCIES
Anne Jäkel, K Alnwick
openalex +1 more source
Pharmacogenetic Interventions, Orphan Groups, and Distributive Justice: The Role of Cost-Benefit Analysis [PDF]
Rai, Arti K.
core +1 more source
Drug Price and Health Policy Knowledge Influence Prescription Behavior in Orphan Diseases: Pheochromocytoma and Paraganglioma As Prototypes of Orphan Drug Econometrics. [PDF]
Le DQ+5 more
europepmc +1 more source
Combined assessment of early and late-phase outcomes in orphan drug development. [PDF]
Pateras K, Nikolakopoulos S, Roes KCB.
europepmc +1 more source
PHP9 BUDGET IMPACT ANALYSIS OF ORPHAN DRUGS IN BELGIUM: ESTIMATES FROM 2008 TO 2013
A. Denis+4 more
openalex +1 more source