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Orphan drug designation and development in Japan: 25 years of experience and assessment
Nature reviews. Drug discovery, 2021K. Sakushima, H. Takeda, Y. Aoi
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Drug Information Journal, 1996
In order to promote the development of orphan drugs, the Pharmaceutical Affairs Law and the Law Concerning the Drug Fund for ADR Relief and R&D Promotion were partially amended in April 1993 and a ...
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In order to promote the development of orphan drugs, the Pharmaceutical Affairs Law and the Law Concerning the Drug Fund for ADR Relief and R&D Promotion were partially amended in April 1993 and a ...
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Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook
Nature reviews. Drug discovery, 2020Anneliene Hechtelt Jonker +8 more
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Determinants of Orphan Drug Prices in Germany
PharmacoEconomics (Auckland), 2020F. Worm, C. Dintsios
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Orphan drugs and orphan diseases
European Journal of Paediatric Neurology, 2000François Feillet +4 more
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Orphan drug development: Challenges, regulation, and success stories
Journal of BiosciencesNarendra Chirmule +4 more
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The Development of Orphan Drugs
2008Approximately 25 million Americans and many more throughout the world suffer from more than 6000 rare diseases. Some of these diseases are wellrecognized, such as Lou Gehrig’s disease or cystic fibrosis, but little is known about many others, such as Adams-Oliver syndrome or Norrie disease.
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