Results 1 to 10 of about 51,209 (99)

[Translated article] Effect of Drug Compounding on Quality of Life in Patients With Genodermatoses: A Cross-Sectional Study

open access: yesActas Dermo-Sifiliográficas, 2022
Background: Cutaneous manifestations are complicated to treat in rare diseases. The main aim of this study was to analyze the impact of compounded drugs prepared by hospital pharmacists on the quality of life of patients with genodermatoses. Material and
M. Oro-Ayude   +4 more
doaj   +1 more source

Clinical experience with orphan drugs for rare metabolic diseases

open access: yesAnales de Pediatría (English Edition), 2022
Introduction: Inborn errors of metabolism are a highly heterogeneous group of orphan diseases. Diet therapy and enzyme and coenzyme replacement are the most frequently used treatment.
Alicia Caso-González   +6 more
doaj   +1 more source

Desafíos en el empleo de los medicamentos huérfanos

open access: yesHumanidades Médicas, 2023
Las enfermedades raras son aquellas que tienen baja prevalencia y que, por lo tanto, el desarrollo de medicamentos para tratarlas no es rentable para las empresas farmacéuticas debido a la baja demanda.
Ivo Heyerdahl-Viau
doaj  

[Potential use of liposomes in tuberculosis treatment]. [PDF]

open access: yesRev Med Inst Mex Seguro Soc, 2023
Jacobo-Delgado YM   +2 more
europepmc   +1 more source

[Intrahepatic Cholestasis and Hyperbilirubinemia Induced by Hyperthyroi- dism: A Case Series]. [PDF]

open access: yesActa Gastroenterol Latinoam, 2023
Garcés JPS   +5 more
europepmc   +1 more source

COVID-19 from a cardiovascular perspective [PDF]

open access: yesArch Cardiol Mex, 2021
Bryce-Moncloa A   +5 more
europepmc   +1 more source

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