Results 291 to 300 of about 7,998,845 (308)

Rare Disease Terminology and Definitions—A Systematic Global Review: Report of the ISPOR Rare Disease Special Interest Group

Value in Health, 2015
Dyfrig A. Hughes, Trevor Richter, Zeba M Khan   +2 more
exaly  

Is leptospirosis a “rare” disease?

Medical Journal of Australia, 1983
openaire   +2 more sources

Therapies for rare diseases: therapeutic modalities, progress and challenges ahead

Nature Reviews Drug Discovery, 2019
Kay Davies, Marco Prunotto, Tudor I Oprea   +2 more
exaly  

THE DOCTOR AND THE RARE DISEASE

Developmental Medicine & Child Neurology, 1985
openaire   +2 more sources

EPIDEMICS OF RARE DISEASES

British Medical Bulletin, 1971
openaire   +2 more sources

China has officially released its first national list of rare diseases

Intractable and Rare Diseases Research, 2018
chunlin Jin, Jiangjiang He, Jiahao Hu
exaly  

Rare disease policies to improve care for patients in Europe

Biochimica Et Biophysica Acta - Molecular Basis of Disease, 2015
Ségolène Aymé
exaly  

Clinical research for rare disease: Opportunities, challenges, and solutions

Molecular Genetics and Metabolism, 2009
Mark L Batshaw, Peter A Merkel, Jeffrey P Krischer   +2 more
exaly  

Clinical Trials in Rare Disease: Challenges and Opportunities

Journal of Child Neurology, 2013
Erika F Augustine, Heather R Adams, Jonathan W Mink   +2 more
exaly  

A Rare Finding of a Rare Disease

Pancreas, 2013
Valerie Anne Fenech, Pierre Ellul, Alexia Abela, Clifford Caruana, Matthew Cassar, Godfrey Laferla   +5 more
openaire   +1 more source