Results 171 to 180 of about 2,038 (184)
Some of the next articles are maybe not open access.
AEs of nusinersen, risdiplam and onasemnogene abeparvovec
Reactions Weekly, 2023openaire +1 more source
Orphan designation: Risdiplam, Treatment of spinal muscular atrophy
Case Medical Research, 2019openaire +2 more sources
Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy
New England Journal of MedicineRichard S, Finkel +7 more
openaire +2 more sources
Risdiplam (spinale Muskelatrophie, < 2 Monate); Nutzenbewertung gemäß § 35a SGB V
2023openaire +1 more source
In brief: Risdiplam (Evrysdi) for spinal muscular atrophy.
The Medical letter on drugs and therapeutics, 2021openaire +1 more source
Risdiplam. SMN2 splicing modulator, Treatment of spinal muscular atrophy
Drugs of the Future, 2019openaire +1 more source
Risdiplam jako innowacja w leczeniu rdzeniowego zaniku mięśni
2023Złotnicka, Zuzanna +5 more
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