Results 191 to 197 of about 2,169 (197)

Evaluation of risdiplam efficacy in 5q spinal muscular atrophy: A systematic comparison of electrophysiologic with clinical outcome measures

European Journal of Neurology
Tobias Kessler, Georges Sam, Wolfgang Wick   +2 more
exaly  

Risdiplam mit überzeugenden Einjahresdaten für die Behandlung der SMA

Pädiatrie, 2019
openaire   +1 more source

Transitioning From Nusinersen to Risdiplam for Spinal Muscular Atrophy in Clinical Practice: A Single‐Center Experience

Muscle and Nerve
Can Ebru Bekircan-Kurt, Garey H Noritz, Kavitha Kotha   +2 more
exaly  

Safety update: risdiplam clinical trial program for spinal muscular atrophy

Safety update: risdiplam clinical trial program for spinal muscular atrophy
Yeung Wai Yin, Baranello Giovanni, Chiriboga Claudia A, Servais Laurent, Darras Basil T, Day John W, Mercuri Eugenio   +6 more
openaire   +1 more source

Further Comments on Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy

New England Journal of Medicine
exaly  

Risdiplam - Ein Hoffnungsträger bei spinaler Muskelatrophie

Österreichische Apothekerzeitung, 2019
openaire   +1 more source

Wirksamkeit von Risdiplam bei Kindern mit SMA bestätigt

DNP – Die Neurologie & Psychiatrie
openaire   +1 more source