Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito +8 more
wiley +1 more source
Impact of a dual-prevention nursing risk-management system on in-hospital adverse events, staff competence, and stakeholder satisfaction: a two-year quasi-experimental implementation study. [PDF]
Li B, Liu J, Tian L, Pang H.
europepmc +1 more source
Uncovering G Protein‐Coupled Receptors: Novel Targets and Biomarkers for Predicting Glioma Prognosis
ABSTRACT Background Low‐grade gliomas (LGG) exhibit significant heterogeneity and recurrence risk. G protein‐coupled receptors (GPCR) contribute to glioma malignant progression, but their prognostic value remains unclear. This work attempts to formulate a GPCR‐based outcome‐predicting model for LGG. Methods Based on TCGA LGG data, the enrichment scores
Jun Yang +4 more
wiley +1 more source
Retraction notice to "Disaster risk management system in Vietnam: progress and challenges" [Heliyon 8 (2022) e10701]. [PDF]
Lan Huong TT +4 more
europepmc +1 more source
Efficacy of a proactive health and safety risk management system in the fire service. [PDF]
Poplin GS +6 more
europepmc +1 more source
ABSTRACT Objectives We aimed to determine the frequency of subclinical optic nerve (ON) lesions using MRI, optical coherence tomography (OCT), and visual evoked potentials (VEP) in radiologically isolated syndrome (RIS), and to assess their diagnostic and prognostic significance.
Christine Lebrun‐Frenay +13 more
wiley +1 more source
Retraction: Risk management system and intelligent decision-making for prefabricated building project under deep learning modified teaching-learning-based optimization. [PDF]
PLOS One Editors.
europepmc +1 more source
The Development of a Risk Management System in the Field of Industrial Safety in the Republic of Kazakhstan. [PDF]
Kudryavtsev SS, Yemelin PV, Yemelina NK.
europepmc +1 more source
ABSTRACT Objective Down syndrome regression disorder is a syndrome characterized by subacute loss of cognitive, behavioral, and functional abilities in individuals with Down syndrome. Electroencephalography abnormalities are frequently observed during evaluation, but it remains unclear whether these findings represent a dynamic marker of disease ...
Jonathan D. Santoro +14 more
wiley +1 more source
Use of the AAPM Safety Profile Assessment Tool to Evaluate the Change in Safety Culture After Implementing the RABBIT Prospective Risk Management System. [PDF]
Ralston A, Yuen J.
europepmc +1 more source

