Results 101 to 110 of about 353 (110)

Sebelipase alfa treatment in a patient with Wolman disease.

2018
Küçükçongar Yavaş, Aynur, Ünal Uzun, Özlem, Ünal, Sevim, Gönülal, Deniz, Siyah Bilgin, Betül, Gündüz, Mehmet   +5 more
openaire   +1 more source

Clinical effect of sebelipase alfa on survival and growth in infants with lysosomal acid lipase deficiency (Wolman disease)

Molecular Genetics and Metabolism, 2014
Vassili Valayannopoulos, Dominique Plantaz, Roshni Vara, Stephen Eckert, Radhika Tripuraneni, Eugene Schneider, Anthony G. Quinn, Kim-Hanh Le Quan Sang, Anaïs Brassier, Jean-Baptiste Arnoux, Fiona White, Catherine Breen, Simon A. Jones   +12 more
openaire   +1 more source

Expert Opinion on Drug Safety

Expert Opinion on Drug Safety
Fatih Ezgü
exaly  

A 14‐step desensitization protocol for sebelipase alfa hypersensitivity in a patient with Wolman disease and secondary hemophagocytic lymphohistiocytosis

Pediatric Allergy and Immunology
Minh H. N. Nguyen, Rachel Bruening, Trent Abel, Shannon Lyons, Brenna Denhardt, Jenna Moore, Panida Sriaroon, Monica Hajirawala, Alexander Y. Kim   +8 more
openaire   +2 more sources

Sebelipase Alfa Normalizes ALT and Multiple other Disease-Related Abnormalities in Patients with LAL-D

MD Conference Express, 2014
openaire   +1 more source

Sebelipase alfa (Kanuma) for lysosomal acid lipase deficiency.

The Medical letter on drugs and therapeutics, 2017
openaire   +1 more source

Effect of sebelipase alfa on liver parameters over 96 weeks in a diverse population of children and adults with lysosomal acid lipase deficiency

Journal of Hepatology, 2018
exaly  

Successful desensitization of sebelipase alfa-induces infusion related reaction in a pediatric patient with Wolman disease.

2020
Küçükçongar Yavaş, Aynur, Ünal Uzun, Özlem, Külhaş Çelik, İlknur, Siyah Bilgin, Betül, Dibek Mısırlıoğlu, Emine   +4 more
openaire   +1 more source

Impact of sebelipase alfa on survival and liver function ininfants with rapidly progressive lysosomal acid lipasedeficiency

2015
Arnoux, Jean, EZGÜ, FATİH SÜHEYL, Valayannopoulos, Vasilli, Brassier, Arnould, Sang, Le Qan, Yang, Yi, Eckert, Stephen, Vara, Roshni, Dominique, Plantaz, Hughes, Jay, Gargus, Jay, zaki, osama, anthony, quinn, sandra, rojas, simon, jones   +14 more
openaire   +1 more source

Review for "A 14-step desensitization protocol for sebelipase alfa hypersensitivity in a patient with Wolman disease and secondary hemophagocytic lymphohistiocytosis"

openaire   +2 more sources