Results 231 to 240 of about 4,840,656 (302)

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24‐Month Follow‐Up From the Italian Registry

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane, Giorgia Coratti, Chiara Cutrì, Antonio Varone, Riccardo Masson, Adele D'Amico, Valeria Sansone, Sonia Messina, Federica Ricci, Chiara Ticci, Claudio Bruno, Caterina Agosto, Francesca Benedetti, Antonella Pini, Sabrina Siliquini, Massimiliano Filosto, Alberto Zambon, Ilaria Bitetti, Maria Rosaria Manna, Claudia Dosi, Riccardo Zanin, Stefano Parravicini, Roberto De Sanctis, Giulia Stanca, Michela Catteruccia, Michele Tosi, Irene Mizzoni, Emilio Albamonte, Valentina Franchino, Maria Sframeli, Ilaria Cavallina, Elena Procopio, Michele Sacchini, Simone Morando, Noemi Brolatti, Federica Trucco, Gaia Scarpini, Elena Briganti, Beatrice Berti, Concetta Palermo, Daniela Leone, Stefano C. Previtali, Eugenio Mercuri, the ITASMAC working group   +43 more
wiley   +1 more source

Short-term effects of video-based education on occupational safety knowledge among commercial divers. [PDF]

Front Public Health
Nishikiori H, Ishitake T.
europepmc   +1 more source

Investigating the impact of migraine on short-term and working memory: a systematic review and meta-analysis. [PDF]

J Neurol
McKay K, Kelly K.
europepmc   +1 more source

Short-term clinical outcomes of balloon-assisted thrombectomy for acute middle cerebral artery occlusive. [PDF]

Front Neurol
Liao B, Yang X, Xing Z, Li G, Liang Z, Deng H, Chen Z, Zhao J, He H, Liang W, Zhu J, Ding Y, He Q, Chen J, Ning W.   +14 more
europepmc   +1 more source

The Ross Renaissance: Trends and Short-Term Outcomes of the Ross Procedure in the United States. [PDF]

JACC Adv
Vadlakonda A, Sakowitz S, Coaston T, Hadaya J, Hinks S, Si MS, Benharash P.   +6 more
europepmc   +1 more source

Short-Term Changes in Retinal Activity With Four Myopia Control Spectacle Lenses. [PDF]

Transl Vis Sci Technol
Fernandes P, Marinho B, Alves-de-Carvalho RS, González-Méijome JM.   +3 more
europepmc   +1 more source

An Appraisal of Short-Term Economic Forecasts [PDF]

Victor Zarnowitz
core  

Tax certainty: proposals for the short term and the long term

Economics: Journal Articles, 2018
Santiago Díaz de Sarralde, Christian von Haldenwang, Tobias Hentze, Nara Monkam   +3 more
doaj  

Amyloid Imaging and APOE Genotype Disclosure and Short-Term Psychological Distress.

JAMA Netw Open
Grill JD, Raman R, Wang S, Ernstrom K, Andrews PS, Appleby BS, Bhangu J, Dhadda S, Irizarry M, Johnson K, Lenio S, MacDonald S, Ramanan VK, Rosenberg PB, Weisman D, Aisen P, Sperling R, Sultzer D, Karlawish J.   +18 more
europepmc   +1 more source