Results 71 to 80 of about 9,502,534 (376)

Evaluation of Children with SMA Type 1 Under Treatment with Nusinersen within the Expanded Access Program in Germany

Journal of Neuromuscular Diseases, 2018
Background: Spinal muscular atrophy (SMA) is a neuromuscular disorder characterized by muscle weakness and muscle atrophy. Nusinersen acts as a splicing modifier and has recently been approved for intrathecal treatment of SMA.
A. Pechmann, T. Langer, D. Schorling, S. Stein, Sibylle Vogt, U. Schara, H. Kölbel, O. Schwartz, A. Hahn, Kerstin Giese, J. Johannsen, J. Denecke, C. Weiss, M. Theophil, J. Kirschner   +14 more
semanticscholar   +1 more source

Stereotactic Body Radiation Therapy for Pediatric, Adolescent, and Young Adult Patients With Osteosarcoma: Local Control Outcomes With Dosimetric Analysis

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Background/Objectives Osteosarcoma is a radioresistant tumor that may benefit from stereotactic body radiation therapy (SBRT) for locoregional control in metastatic/recurrent disease. We report institutional practice patterns, outcomes, toxicity, and failures in osteosarcoma patients treated with SBRT.
Jenna Kocsis, Shauna R. Campbell, Jonathan Jang, Eashwar Somasundaram, Chandana A. Reddy, Jacob G. Scott, Lilyana Angelov, Peter M. Anderson, Matteo Trucco, Zachary Burke, Lukas Nystrom, Nathan Mesko, Anthony Magnelli, Erin S. Murphy   +13 more
wiley   +1 more source

THE TADPOLE OF THE MEXICAN TREE FROG CHARADRAHYLA TAENIOPUS (ANURA: HYLIDAE)

Caldasia, 2015
The tadpole of Charadrahyla taeniopus is described. This tadpole is a typical stream-dweller with a long depressed body, oral disc completely surrounded by marginal papillae with numerous small submarginal papillae lateral to the mouth, and several rows ...
MOISES KAPLAN, PETER HEIMES
doaj   +1 more source

Lifestyle Behaviors and Cardiotoxic Treatment Risks in Adult Childhood Cancer Survivors

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Background Higher doses of anthracyclines and heart‐relevant radiotherapy increase cardiovascular disease (CVD) risk. This study assessed CVD and CVD risk factors among adult childhood cancer survivors (CCSs) across cardiotoxic treatment risk groups and examined associations between lifestyle behaviors and treatment risks.
Ruijie Li, Raquel Revuelta Iniesta, Alan R. Barker, Dimitris Vlachopoulos, Tomáš Sláma, Christina Schindera, Fabiën N. Belle   +6 more
wiley   +1 more source

The clinical landscape for SMA in a new therapeutic era

Gene Therapy, 2017
Despite significant advances in basic research, the treatment of degenerative diseases of the nervous system remains one of the greatest challenges for translational medicine.
K. Talbot, E. Tizzano
semanticscholar   +1 more source

Changes in Body Composition in Children and Young People Undergoing Treatment for Acute Lymphoblastic Leukemia: A Systematic Review and Meta‐Analysis

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Ongoing evidence indicates increased risk of sarcopenic obesity among children and young people (CYP) with acute lymphoblastic leukemia (ALL), often beginning early in treatment, persisting into survivorship. This review evaluates current literature on body composition in CYP with ALL during and after treatment.
Lina A. Zahed, Raquel Revuelta Iniesta, Mary Fewtrell, Julie Lanigan, Breeana Gardiner, Graeme O'Connor   +5 more
wiley   +1 more source

THE IMPLEMENTATION OF TEACHING SPEAKING AT SMA ISLAM\ud KEPANJEN [PDF]

, 2007
The objectives of this study were 1) to know the objective of teaching speaking at SMA Islam Kepanjen, 2) to know the topic covered in teaching speaking at SMA Islam Kepanjen, 3) to know the technique of teaching speaking at SMA Islam Kepanjen, 4) to ...
Rismawati, Aini
core  

Precise Identifications of Submillimeter Galaxies: Measuring the History of Massive Star-Forming Galaxies to z>5

, 2013
We carried out extremely sensitive Submillimeter Array (SMA) 340 GHz (860 micron) continuum imaging of a complete sample of SCUBA 850 micron sources (>4 sigma) with fluxes >3 mJy in the GOODS-N.
A. J. Barger, Alexander, Alexander, Appleton, Barger, Barger, Barger, Barger, Barger, Bautz, Bell, Bertoldi, Blain, Blain, Bothwell, Briggs, C.-C. Chen, Capak, Carilli, Chapman, Chapman, Chapman, Chen, Cowie, Cowie, Cowie, Daddi, Daddi, Dannerbauer, Dannerbauer, Dannerbauer, Downes, Eales, Eales, Eddington, F. N. Owen, Fixsen, Fomalont, Giavalisco, Hatsukade, Hauser, Ho, Hopkins, Iono, J. P. Williams, Karim, Kennicutt, Klaas, Knudsen, Kovács, L. L. Cowie, Larson, Lindner, Momjian, Morrison, Owen, Pascale, Pope, Puget, Reddy, Riechers, Sargent, Sargent, Schinnerer, Severgnini, Smail, Smolčić, Smolčić, Swinbank, W.-H. Wang, Wang, Wang, Wang, Wang, Wang, Wang, Webb, Weiß, Wold, Younger, Younger, Yun   +81 more
core   +1 more source

Parent‐to‐Child Information Disclosure in Pediatric Oncology

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Background Despite professional consensus regarding the importance of open communication with pediatric cancer patients about their disease, actual practice patterns of disclosure are understudied. Extant literature suggests a significant proportion of children are not told about their diagnosis/prognosis, which is purported to negatively ...
Rachel A. Kentor, Flora Hoodin, Michelle Byrd, Kristin A. Kullgren, Leah LaLonde, Lauren Benkoske, Patrick Smith, Dawn Carson, Karen MacDonald, Susumu Inoue, Brenda Kitchen, Kate Gowans, Gregory A. Yanik   +12 more
wiley   +1 more source

Effect of the Butyrate Prodrug Pivaloyloxymethyl Butyrate (AN9) on a Mouse Model for Spinal Muscular Atrophy. [PDF]

, 2016
Spinal muscular atrophy (SMA) is an early-onset motor neuron disease that leads to loss of muscle function. Butyrate (BA)-based compounds markedly improve the survival and motor phenotype of SMA mice.
Butchbach, Matthew E.R., Edwards, Jonathan D.   +1 more
core   +2 more sources