Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito +8 more
wiley +1 more source
Spatial spillover effects of green public investment on regional sustainable development: An analysis based on spatial econometric models. [PDF]
Tong S, Haiqing H, Xinyue Q.
europepmc +1 more source
ABSTRACT Objectives We aimed to determine the frequency of subclinical optic nerve (ON) lesions using MRI, optical coherence tomography (OCT), and visual evoked potentials (VEP) in radiologically isolated syndrome (RIS), and to assess their diagnostic and prognostic significance.
Christine Lebrun‐Frenay +13 more
wiley +1 more source
Evaluation of carbon sustainable development in the nine provinces and regions of the Yellow River Basin based on carbon ecological footprints. [PDF]
Gan R +5 more
europepmc +1 more source
Sustainable development of China's aesthetic teaching in long-term policy changes. [PDF]
Wang X, Chen X, Qin P, Lu J, Wang H.
europepmc +1 more source
Sustainable development evaluation of agri-culture-tourism integration in revolutionary old areas: a case study of Tianshui city. [PDF]
Luo M, Zhang H, Xuan M, Liu T, Zhou Q.
europepmc +1 more source
Sustainable development in mosque construction. [PDF]
Yu H, Zahidi I, Fai CM, Madsen DØ.
europepmc +1 more source
Chatting with an LLM-based AI elicits affective and cognitive processes in education for sustainable development. [PDF]
Spangenberger P +4 more
europepmc +1 more source
Global forest conservation policies and the Sustainable Development Goals
Britz W, Wilts R, Wuepper D.
europepmc +1 more source

