Results 211 to 216 of about 47,298 (216)

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

Lancet Neurology, The, 2010
David J Birnkrant, Laura E. Case, Paula R Clemens   +2 more
exaly  

Short Telomeres and Stem Cell Exhaustion Model Duchenne Muscular Dystrophy in mdx/mTR Mice

Cell, 2010
Alessandra Sacco, Foteini Mourkioti, Scott L Delp   +2 more
exaly  

Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

New England Journal of Medicine, 2017
Richard S Finkel, Eugenio Mercuri, Basil T Darras   +2 more
exaly  

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

New England Journal of Medicine, 2017
Richard Shell, Linda P Lowes, Lindsay N Alfano   +2 more
exaly  

AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial

Nature Medicine
Jerry Mendell, Francesco Muntoni, Craig M Mcdonald   +2 more
exaly  

Advances in Duchenne muscular dystrophy gene therapy

Nature Reviews Genetics, 2003
exaly