Results 281 to 290 of about 181,456 (327)

Thalassemias

Pediatric Clinics of North America, 2013
The thalassemia syndromes are hemoglobin disorders that result from significantly reduced or absent synthesis of either the α- or β-globin chains. The result is a chronic hemolytic anemia with ineffective erythropoiesis and bone marrow overstimulation.
Alissa, Martin, Alexis A, Thompson
openaire   +2 more sources

Alpha‐thalassemia

American Journal of Hematology, 1977
AbstractThe current concepts of α‐thalassemia including incidence, genetics, clinical spectrum and diagnosis are reviewed. Speculation concerning clinical application of the molecular biology of α‐thalassemia is also presented.
J G, Adams, M H, Steinberg
openaire   +2 more sources

Thalassemia

Hematology/Oncology Clinics of North America, 2023
Edward J, Benz, Vijay G, Sankaran
openaire   +2 more sources

Thalassemia

Pathology, 1984
M, Poncz, A, Cohen, E, Schwartz
openaire   +4 more sources

Thalassemia

Annual Review of Medicine, 1975
B G, Forget, D G, Nathan
openaire   +2 more sources

Thalassemia

New England Journal of Medicine, 1972
Daniel Deykin, Christine Balko, David G. Nathan   +2 more
openaire   +2 more sources

CRISPR–Cas9-mediated gene editing of the BCL11A enhancer for pediatric β0/β0 transfusion-dependent β-thalassemia

Nature Medicine, 2022

exaly  

Gene replacement of α-globin with β-globin restores hemoglobin balance in β-thalassemia-derived hematopoietic stem and progenitor cells

Nature Medicine, 2021
Michael Cromer, Joab Camarena, Renata M Martin   +2 more
exaly  

Thalassemia

Annals of Ophthalmology, 2006
openaire   +3 more sources

Lentiviral globin gene therapy with reduced-intensity conditioning in adults with β-thalassemia: a phase 1 trial

Nature Medicine, 2022
Aurelio Maggio, Friederike Kogel, Susan Prockop   +2 more
exaly