Gene Editing for Haemophilia—The Next Frontier
ABSTRACT The recently approved haemophilia A and B gene therapies via adeno‐associated virus (AAV) showed a promising therapeutic response after a single injection, but there are still limitations, including the potential loss of transgene expression and restriction in adults.
Mirko Pinotti +3 more
wiley +1 more source
Associations of Baseline Cognitive and Psychosocial Function with Clinical Outcomes After Autologous Stem Cell Transplantation in a Multiple Myeloma Sample. [PDF]
Rueda-Lara M +12 more
europepmc +1 more source
This is a retrospective review of intestinal tract biopsies from patients treated with various cellular immunotherapies (BCMA and CD19‐directed CAR T, teclistamab and rituximab therapies). We found distinct but overlapping histologic patterns across treatment groups, with lamina propria plasma cell depletion, crypt apoptotic bodies and active ...
Olivia J Leung +7 more
wiley +1 more source
Vertebral trabecular attenuation serial changes on chest CT after autologous hematopoietic stem cell transplantation. [PDF]
Atçeken Z +5 more
europepmc +1 more source
Incident Hepatitis B Virus Infection after Hematopoietic Stem Cell Transplantation in Initially HBV-Seronegative Recipients: Four Cases. [PDF]
Chen D, Yu L, Yao F, Xu H.
europepmc +1 more source
Timing of autologous stem cell transplantation and induction response in central nervous system lymphoma. [PDF]
Higuchi Y +11 more
europepmc +1 more source
Autologous stem cell transplantation versus consolidation chemotherapy as postremission treatment in newly diagnosed favorable- and intermediate-risk patients with AML: A comparative analysis of HOVON-SAKK-Nordic trials. [PDF]
Kotsos D +17 more
europepmc +1 more source
Is there a role for immune checkpoint inhibitors in high-risk medulloblastoma beyond the salvage setting? [PDF]
Wang YL +4 more
europepmc +1 more source
Adipose Stem Cell Mitochondrial Transplantation in ART: From Biological Rationale to Clinical Milestone. [PDF]
Wijethunga Arachchilage HPK +3 more
europepmc +1 more source

