Results 201 to 210 of about 7,799 (249)

Myonuclear domain-associated and central nucleation-dependent spatial restriction of dystrophin protein expression in a novel DMD mouse model

Chwalenia K, Feng V, Hemmer N, Hildyard JC, Roskrow LE, Piercy RJ, Wang ET, Aartsma-Rus A, van Putten M, Wood MJ, Roberts TC.   +10 more
europepmc   +1 more source

Gene therapy delivered micro-dystrophins co-localize with transgenic utrophin in dystrophic skeletal muscle fibers. [PDF]

Neuromuscul Disord
Krishna S, Piepho AB, Lake DM, Cumby LR, Lortz KK, Lowe J, Chamberlain JS, Rafael-Fortney JA.   +7 more
europepmc   +1 more source

The effects of anti-IL-6 receptor antibody on muscle pathology in dystrophin/utrophin dKO mice

, 2017
E. Wada, Tanihata Jun, Akira Iwamura, Takeda Shinichi, Hayashi Yukiko K, Ryoichi Matsuda   +5 more
openalex   +1 more source

On RNA-programmable gene modulation as a versatile set of principles targeting muscular dystrophies. [PDF]

Mol Ther
Capelletti S, García Soto SC, Gonçalves MAFV.   +2 more
europepmc   +1 more source

Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review. [PDF]

BioDrugs
Szwec S, Kapłucha Z, Chamberlain JS, Konieczny P.   +3 more
europepmc   +1 more source

Unlocking the genetic blueprint of duchenne muscular dystrophy: A personalized approach with MLPA and WES. [PDF]

Glob Med Genet
Mathur P, Kaur A, Agarwal KK, Agarwal LK, Mathur A, Choudhary D.   +5 more
europepmc   +1 more source

A Scoping Review of Sarcoglycan Expression in Non-Muscle Organs: Beyond Muscles. [PDF]

Biomolecules
Nicita F, Freni J, Centofanti A, Favaloro A, Labellarte D, Cutroneo G, Anastasi MR, Vermiglio G.   +7 more
europepmc   +1 more source

Pharmacological Treatments and Therapeutic Targets in Muscle Dystrophies Generated by Alterations in Dystrophin-Associated Proteins. [PDF]

Medicina (Kaunas)
Luna-Angulo A, Landa-Solís C, Escobar-Cedillo RE, Estrada-Mena FJ, Sánchez-Chapul L, Gómez-Díaz B, Carrillo-Mora P, Avilés-Arnaut H, Jiménez-Hernández L, Jiménez-Hernández DA, Miranda-Duarte A.   +10 more
europepmc   +1 more source

CRISPR-Cas9 mediated endogenous utrophin upregulation improves Duchenne Muscular Dystrophy

, 2023
Guiraud S, Dastidar S, Mazed F, Amor F, Ralu M, de Cian A, Richard I, Ronzitti G, Tedesco FS, Amendola M.   +9 more
europepmc   +1 more source

Impaired bone defect and fracture healing in dystrophin/utrophin double-knockout mice and the mechanism.

, 2020
Xueqin Gao, Xuying Sun, Sarah Amra, Yan Cui, Zhenhan Deng, Haizi Cheng, Greg Zhang, Charles Huard, Bing Wang, Johnny Huard   +9 more
openalex   +1 more source