Results 131 to 140 of about 2,730,603 (357)
The Validity of Papal Claims. F. Nutcombe OxenhamA Short History of the Book of Common Prayer: With an Appendix Containing the Prayers of "The Book Annexed". William Reed Huntington [PDF]
Alfred Wesley Wishart
openalex +1 more source
Long‐Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons
ABSTRACT Objectives This ongoing, open‐label extension study is evaluating the long‐term safety, tolerability, and efficacy of givinostat, a Class I and II histone deacetylase inhibitor, in patients with Duchenne muscular dystrophy (DMD). Methods The recruited patients completed one of two prior clinical studies (one Phase 2 and one Phase 3 [EPIDYS ...
Craig M. McDonald+74 more
wiley +1 more source
This research considers the validity of tutor assessed, pre-university independent research reports. Evidence of construct relevance in tutors’ interpretations of the levels awarded to the candidates’ research process was investigated.
Jackie Greatorex, Stuart Shaw
doaj
THE VALIDITY OF DETERMINATIONS OF THE COLLOID OSMOTIC PRESSURE OF SERUM
Abby H. Turner
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Durability of Response to B‐Cell Maturation Antigen‐Directed mRNA Cell Therapy in Myasthenia Gravis
ABSTRACT Objective We report the 12‐month follow‐up outcomes from a Phase 2 clinical trial (NCT04146051) evaluating Descartes‐08, a BCMA‐directed RNA chimeric antigen receptor T‐cell (rCAR‐T) therapy for refractory generalized myasthenia gravis (MG).
Nizar Chahin+10 more
wiley +1 more source
Fourth Report Of The Private International Law Committee (Formal Validity Of Wills) [PDF]
J. H. C. Morris
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Assessing a Mitochondrial Disease Treatment via a Novel Statistical Technique for Accelerometer Data
ABSTRACT Objective Therapeutic development for mitochondrial diseases, rare genetic disorders with pathogenic defects of oxidative phosphorylation, is hindered by unsatisfactory outcome measures. To address this problem, we provide the first clinical application of a novel, bias‐adjusted outcome measure of acceleration across a range of subjects ...
Ian W. McKeague+8 more
wiley +1 more source
ABSTRACT Background Managing long COVID in people with multiple sclerosis and related disorders (pwMSRD) is complex due to overlapping symptoms. To address evidence gaps, we evaluated long COVID susceptibility in pwMSRD versus controls and its associations with multi‐domain function and disability.
Chen Hu+15 more
wiley +1 more source