Results 111 to 120 of about 1,367 (120)

Durability of Voretigene Neparvovec for Biallelic RPE65-Mediated Inherited Retinal DiseasePhase 3 Results at 3 and 4 Years

Ophthalmology, 2021
Purpose: To determine whether functional vision and visual function improvements after voretigene neparvovec (VN; Luxturna [Spark Therapeutics, Inc]) administration in patients with biallelic RPE65 mutation-associated inherited retinal disease are ...
Francesca Simonelli, Amy Tillman, Daniel C Chung   +2 more
exaly   +2 more sources

Objective Outcomes to Evaluate Voretigene Neparvovec Treatment Effects in Clinical Practice

Ophthalmology Retina
Aim: To assess the efficacy of Voretigene Neparvovec (VN) treatment by objective fixation stability and chromatic pupillometry testing in clinical practice. Design: Retrospective cohort study with longitudinal follow-up. Subjects: Twelve patients (aged 7
Francesca Simonelli, Francesco Testa, Paolo Melillo   +2 more
exaly   +2 more sources

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Gene Therapy with Voretigene Neparvovec Improves Vision and Partially Restores Electrophysiological Function in Pre-School Children with Leber Congenital Amaurosis

Biomedicines, 2023
Stylianos Michalakis, Herbert Jägle, Carsten Framme   +2 more
exaly  

Short term morphological rescue of the fovea after gene therapy with voretigene neparvovec

Acta Ophthalmologica, 2022
Friederike Kortuem, Ronja Jung, Susanne Kohl   +2 more
exaly  

Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation–Associated Inherited Retinal DystrophyResults of Phase 1 and 3 Trials

Ophthalmology, 2019
Francesca Simonelli, Katherine A. High, Amy Tillman   +2 more
exaly  

Classification and Growth Rate of Chorioretinal Atrophy after Voretigene Neparvovec-Rzyl for -Mediated Retinal Degeneration

Ophthalmology Retina
Nikhil Bommakanti, Çağrı G. Beşirli, Aaron Nagiel   +2 more
exaly  

Efficacy and Safety of Voretigene Neparvovec in RPE65-Retinopathy: Results of a Phase III Trial in Japan

Ophthalmology Science
Kunihiko Akiyama, Kaoru Fujinami
exaly  

RPE65-Associated Retinal Dystrophies: Phenotypes and Treatment Effects with Voretigene Neparvovec

Klinische Monatsblatter Fur Augenheilkunde
Katarina Stingl, Claudia Priglinger, Philipp Herrmann   +2 more
exaly  

Single Center Experience with Voretigene Neparvovec Gene Augmentation Therapy in RPE65 Mutation–Associated Inherited Retinal Degeneration in a Clinical Setting

Ophthalmology
Frank G Holz, Markus Preising, Birgit Lorenz   +2 more
exaly  

Gene Therapy with Voretigene Neparvovec (Luxturna®)

Siegfried Priglinger
exaly